[Federal Register: August 5, 2003 (Volume 68, Number 150)]
[Rules and Regulations]               
[Page 46363-46402]
From the Federal Register Online via GPO Access [wais.access.gpo.gov]
[DOCID:fr05au03-14]                         
 
 
[[Page 46363]]
 
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Part III
 
Department of Health and Human Services
 
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Food and Drug Administration
 
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21 CFR Part 172
 
Food Additives Permitted for Direct Addition to Food for Human 
Consumption; Olestra; Final Rules
 
 
[[Page 46364]]
 
 
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DEPARTMENT OF HEALTH AND HUMAN SERVICES
 
Food and Drug Administration
 
21 CFR Part 172
 
[Docket No. 2000F-0792]
 
 
Food Additives Permitted for Direct Addition to Food for Human 
Consumption; Olestra
 
AGENCY: Food and Drug Administration, HHS.
 
ACTION: Final rule.
 
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SUMMARY: The Food and Drug Administration (FDA) is amending the food 
additive regulations to remove the requirement for the label statement 
prescribed specifically for savory snack products that contain olestra. 
This action is in response to a petition filed by the Procter and 
Gamble Co.
 
DATES: The regulation is effective August 5, 2003. Submit written 
objections and requests for a hearing by September 4, 2003.
 
ADDRESSES: Submit written objections to the Division of Dockets 
Management (HFA-305), Food and Drug Administration, rm. 1061, 5630 
Fishers Lane, Rockville, MD 20852. Submit electronic objections to 
http://www.fda.gov/dockets/ecomments.
 
FOR FURTHER INFORMATION CONTACT: Mary D. Ditto, Center for Food Safety 
and Applied Nutrition (HFS-255), Food and Drug Administration, 5100 
Paint Branch Pkwy., College Park, MD 20740-3835, 202-418-3102.
 
SUPPLEMENTARY INFORMATION: 
 
Table of Contents
 
I. Subject of Petition
II. Background
    A. Basis for Requiring the Label Statement--1996 Decision
    1. Legal Authority for the 1996 Label Statement
    2. GI Issues Associated With Olestra
    3. Nutritional Issues Associated With Olestra
    B. Opportunity for Comment and Consideration of New Data
    1. Request for Comments on Label Statement Required by the 1996 
Final Rule
    2. P&G's Commitment To Further Studies
    3. FDA's Commitment to Convene an FAC Meeting
    4. P&G's Petition To Remove the Requirement for the Label 
Statement
    5. Comments Received
III. Data and Information Since the 1996 Final Rule
    A. Introduction
    B. Surveys and Postmarket Passive Surveillance Regarding GI 
Effects
    1. Telephone Surveys Regarding GI Complaints
    a. P&G
 
    b. CSPI
    2. Postmarket Passive Surveillance by P&G
    3. Postmarket Surveillance Reports From CSPI
    4. Comments Regarding Consumer Reports
    C. Studies Regarding GI Effects
    1. Rechallenge Study
    2. Acute Consumption Study
    3. Home Consumption Study
    4. Stool Composition Study
    5. Comments Regarding the GI Studies
    D. A Study Regarding Nutritional Effects--Active Surveillance
    1. Active Surveillance Study by P&G
    2. Comments Regarding the Active Surveillance Study
    E. Consultations and Literature Review Regarding Nutritional 
Effects
    F. Consumer Perception Studies of the Label Statement
    1. 1996 Consumer Studies
    2. 1999 Consumer Studies
    G. 1998 FAC Discussion of the Label Statement
IV. FDA's Conclusions
    A. The Applicable Legal Standard
    B. FDA's Conclusions Regarding Gastrointestinal Effects
    1. Basis of the 1996 Final Rule--GI Effects
    a. Abdominal cramping
    b. Loose stools
    2. Data in the Current Petition--GI Effects
    a. Abdominal cramping
    b. Loose stools
    C. FDA's Conclusions Regarding Nutritional Effects
    1. Basis of the 1996 Final Rule--Nutritional Effects
    2. Data in the Current Petition--Nutritional Effects
V. Response to Comments on the Label
    A. Label Statement for GI Effects
    B. Label Statement for Nutritional Effects
    C. Labeling for Special Populations
    D. Label Statement in Its Entirety
    E. Data and Information Considered in this Rulemaking
    F. Safety of Olestra
    G. Allergenicity of Olestra or Olestra-Containing Foods
    H. Nutrition Labeling and Claims
    I. Appearance of the Label Statement
    J. Labeling for Single-Serving Packages
    K. 1995 and 1998 FAC Meetings
VI. Summary
VII. Environmental Impact
VIII. Inspection of Documents
IX. Objections
X. References
 
I. Subject of Petition
 
    In a notice in the Federal Register of March 3, 2000 (65 FR 11585-
11586), FDA announced that a food additive petition had been filed by 
the Procter & Gamble Co., 6071 Center Hill Ave., Cincinnati, OH 45224 
(P&G, the petitioner) proposing that the food additive regulations be 
amended in Sec.  172.867 Olestra (21 CFR 172.867) to remove the 
requirement for the label statement prescribed in Sec.  172.867(e).
 
II. Background
 
    In the Federal Register of January 30, 1996 (61 FR 3118, ``the 1996 
final rule'') FDA announced the approval of olestra for use as a fat 
substitute in prepackaged ready-to-eat savory snacks. Olestra is the 
common name for a mixture of substances formed by chemical combination 
of sucrose with six, seven, or eight fatty acids. The fatty acids, 
bound to sucrose by ester bonds, are derived from edible fats and oils.
    Olestra is essentially not absorbed or metabolized and passes 
unchanged through the gastrointestinal (GI) system (61 FR 3118 at 3125-
3127). Therefore, olestra has the potential to affect GI physiology and 
function. Additionally, because of olestra's physical properties, fat-
soluble nutrients present in olestra-containing foods \1\ or other 
foods in the GI tract at the same time as olestra can partition into 
olestra and pass through the GI tract without being absorbed by the 
body. Therefore, FDA required the addition of fat-soluble vitamins A, 
D, E, and K, to savory snacks containing olestra to compensate for any 
inhibition of absorption by olestra (Sec.  172.867(d)).
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    \1\ Olestra has only been approved for use as a fat substitute 
in savory snacks. Throughout this document, we refer to olestra-
containing foods to include those savory snacks made with olestra as 
well as other olestra-containing foods used in the preapproval 
studies for olestra.
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    At the time of the 1996 final rule, FDA concluded that, to avoid 
being misbranded within the meaning of sections 201(n) and 403(a)(1) of 
the Federal Food, Drug, and Cosmetic Act (the act) (21 U.S.C. 321(n) 
and 343(a)(1)), olestra-containing foods would need to bear a label 
statement to inform consumers about possible effects of olestra on the 
GI system. The label statement also would clarify that the added 
vitamins were present to compensate for any nutritional effects of 
olestra, rather than to provide enhanced nutritional value. Therefore, 
the 1996 final rule required that foods containing olestra be labeled 
with the following statement in a boxed format: ``THIS PRODUCT CONTAINS 
OLESTRA. Olestra may cause abdominal cramping and loose stools. Olestra 
inhibits the absorption of some vitamins and other nutrients. Vitamins 
A, D, E, and K have been added.'' (Sec.  172.867(e)(1)). FDA included 
the term ``other nutrients'' because any nutrient that is as lipophilic 
as these vitamins would also be affected, although there was no known 
basis for adding such nutrients back. The agency also required that the 
statement be made in a standardized format that specifies, among other 
things, type style and type size, and that
 
[[Page 46365]]
 
the label statement be surrounded by a box to ensure proper prominence. 
This requirement was established under section 409(c)(3)(B) of the act 
(21 U.S.C. 348(c)(3)(B)), which prohibits approval of a food additive 
if the proposed use would result in misbranding of food (61 FR 3118 at 
3160). The legal authority and scientific basis that underlaid the 
requirement for this label statement are reviewed in detail in the next 
section of this document.
 
A. Basis for Requiring the Label Statement--1996 Decision
 
1. Legal Authority for the 1996 Label Statement
    Under section 403(a)(1) of the act, a food is deemed to be 
misbranded if its labeling is false or misleading in any particular. 
Section 201(n) of the act amplifies what is meant by ``misleading.'' 
Section 201(n) of the act states that in determining whether labeling 
is misleading, the agency shall take into account not only 
representations made or suggested about the product, but also the 
extent to which the labeling fails to reveal facts material in light of 
such representations or material with respect to consequences which may 
result from use under the conditions of use prescribed in the labeling 
or under such conditions of use as are customary or usual (see 21 CFR 
1.21). Thus, the omission of such material fact from the label or 
labeling of a food causes the product to be misbranded within the 
meaning of sections 201(n) and 403(a)(1) of the act.
2. GI Issues Associated With Olestra
    As noted, olestra is not digested or absorbed, and it passes 
through the GI tract intact. The petitioner conducted a number of 
studies to address issues of potential concern with respect to the 
effect of olestra as it passes through the GI tract (61 FR 3118 at 
3152-3159). For example, during studies designed primarily to assess 
potential effects of olestra on absorption of fat-soluble dietary 
components present in the gut at the same time, the petitioner also 
assessed the potential for olestra to elicit GI symptoms such as 
cramping, bloating, loose stools, and diarrhea-like symptoms by 
collecting reports from participants in the studies. In two human 
nutritional studies \2\ (88 and 100 subjects respectively), the entire 
diet of the subjects was controlled during the length of an 8-week 
study period. The studies were parallel, double-blind, and placebo-
controlled, with olestra dosages of 0 (placebo), 8, 20, and 32 grams 
per day (g/d).\3\ The diets were formulated so that the total 
digestible fat (triglyceride) content was the same for all treatment 
groups. Triglyceride was added into the diets in the form of butter, 
margarine, or vegetable oil to compensate for the amount of fat 
replaced by olestra in the olestra-containing foods. Olestra was added 
to various food items by substituting olestra for triglyceride in 
recipes or in cooking oils. Therefore, the total amount of lipid-like 
material (digestible triglyceride plus olestra) increased with 
increasing olestra dose. Each meal contained olestra or the 
corresponding placebo (triglyceride). Subjects were questioned daily 
about changes in their health, including GI symptoms. To facilitate 
collection of GI symptom data, a questionnaire provided a list of 
common GI symptoms along with general definitions of each and was 
completed by each subject to capture data about the type, severity, and 
duration of symptoms experienced. As noted in the 1996 final rule (61 
FR 3118 at 3152), the petitioner stated that the two 8-week studies 
were not intended to examine GI symptoms under real-life consumption 
conditions where snacks are not consumed every day with every meal and 
where people may moderate intake if they experience GI symptoms.
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    \2\ In evaluating olestra's nutritional effects, the petitioner 
conducted two 8-week clinical studies, the 8-week clinical dose 
response study (8-week DR), and the 8-week clinical vitamin 
restoration study (8-week VR)(61 FR 3118 at 3133-3134). In this 
document, when discussing the combined results of these studies, 
they will be called the two 8-week studies.
    \3\ By comparison, FDA concluded that the estimated lifetime-
averaged daily intake at the 90th percentile of olestra consumption 
would be 7.0 grams per person per day (g/p/d) (61 FR 3118 at 3124).
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    FDA's analysis of the data from the two 8-week studies (61 FR 3118 
at 3152-3154) showed that there was a dose-response effect for olestra 
with respect to two endpoints, reported diarrhea/loose stools and fecal 
urgency. Reporting of diarrhea was based on subjects' perception of 
diarrhea. FDA found no evidence that study subjects experiencing 
olestra-related symptoms described as ``diarrhea'' also experienced 
significant fluid or significant electrolyte loss. The effect of 
olestra on stool consistency is similar to that produced by liquid 
petrolatum, which softens fecal contents. FDA recognized that the 
effect observed was not diarrhea in the clinical sense, but used that 
term in the 1996 final rule, and is using that term here, because it is 
the term used in the study report. FDA also found that these GI 
symptoms cease soon after olestra is no longer consumed.
    The petitioner also conducted a study, the Fecal Parameters Study, 
designed to examine fecal composition of stools from subjects who 
reported diarrhea when consuming olestra (61 FR 3118 at 3155). The 
study consisted of two phases, a screening phase and a study phase. The 
screening phase was conducted to identify subjects who reported GI 
symptoms from olestra consumption. During the study phase, the 
identified subjects ate different amounts of olestra, and GI symptoms 
were recorded and fecal measurements were made. From the initial 
screening phase, eighteen subjects reported an increase in the 
frequency, severity, or duration of GI symptoms during the olestra 
period, relative to the placebo period. These 18 subjects were selected 
to take part in the study phase, and 15 completed the study. The study 
phase was a crossover, placebo-controlled, single-blind (subject) 
design with three treatment groups, 0, 10, and 20 g/d olestra. Each 
subject received each treatment for 7 days. The treatment periods were 
separated by 7-day washout periods. Subjects ate all treatment meals 
under supervision at the clinical site, and ate their habitual diets at 
home during the washout periods. Study subjects recorded GI symptoms 
daily. Total fecal collections were made the last 3 days of each 
treatment period. Daily stool collections were measured for wet weight, 
volume, and density, and the pooled three day samples were analyzed for 
water concentration, dry weight, olestra content, sodium (Na), 
potassium (K), chloride (Cl), total and individual bile salts, free 
fatty acids, triglycerides, and total lipids.
    Measurements of the concentration of stool water and electrolytes 
(Na, K, and Cl) suggested that these parameters did not differ in the 
stools of persons reporting ``diarrhea'' during the olestra 20 g/d 
period from those in the nondiarrheal stools (during the placebo 
period) of the same persons. However, it was not possible to analyze 
stool electrolyte values by individual stools or by individual days 
because the stools were pooled from the 3-day collection period, as is 
normally done when measuring fecal parameters. FDA noted that there 
appeared to be an increased weight of stools in those subjects 
reporting ``diarrhea'' when eating 20 g/d olestra that is not 
completely accounted for by the presence of olestra in the stools. FDA 
concluded that the results of this study indicated that there is no 
difference in stool composition (e.g., water and electrolyte content) 
when subjects consumed olestra versus placebo (61 FR 3118 at 3155).
    FDA found that the number of subjects in the Fecal Parameters Study
 
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who reported diarrhea increased with increasing dose of olestra (i.e., 
3 subjects (20 percent) in the placebo, 6 subjects (40 percent) who 
consumed 10 g of olestra, and 11 subjects (69 percent) who consumed 20 
g of olestra). In addition, both the mean number of reported diarrheal 
bowel movements per subject reporting any diarrhea, and the severity of 
the reported diarrhea, increased with increasing olestra consumption. 
Although there was an increase in the number of subjects reporting 
loose stools with increasing olestra dose, this increase was not 
statistically significant. FDA concluded that these results were 
qualitatively similar to the results of the 8-week studies.
    The agency concluded, based upon its evaluation of the data and 
information available at the time, that consumption of olestra causes 
GI effects such as loose stools, abdominal cramping, and diarrhea-like 
symptoms. Additionally, the agency concluded that while olestra caused 
these GI symptoms, there was no evidence that these effects represented 
adverse health consequences.
    At the time of approval, the agency did not have information about 
the potential GI effects from usual or customary consumption of olestra 
in savory snacks. Nonetheless, FDA considered it prudent to rely on the 
available data in deciding whether a label statement about olestra's 
potential effects on the GI tract was necessary. Olestra had the 
potential to be consumed in relatively large quantities by every 
segment of the U.S. population. Additionally, because olestra had never 
before been available in the marketplace, consumers had no experience 
with it and were not familiar with it or its potential to cause GI 
effects. The agency believed that providing consumers label information 
about olestra's GI effects would preclude unnecessary concerns about 
the origin of GI effects, were they to be observed, and might also 
prevent unnecessary or inappropriate medical treatment of those 
symptoms (61 FR 3118 at 3161). Based on the weight of the evidence 
about olestra's potential to cause GI effects, as well as the agency's 
belief that consumers lacked familiarity with olestra and its potential 
to cause such effects, FDA concluded at the time of olestra's approval 
that the relationship between GI symptoms and consumption of foods 
containing olestra is a fact that is material in light of the 
consequences of consuming olestra, and therefore a label statement was 
required.
3. Nutritional Issues Associated With Olestra
    FDA concluded that olestra inhibits the absorption of the fat-
soluble components of the diet when these components are present in the 
GI tract simultaneously with olestra (61 FR 3118 at 3132-3147). Such 
components include the fat-soluble vitamins A, D, E, and K, and the 
lipophilic carotenoids. Based on the data from the nutritional studies, 
FDA concluded that addition of the four fat-soluble vitamins (A, D, E, 
K) to foods containing olestra would compensate for any decreased 
absorption due to the action of olestra, thus ensuring that consumption 
of an olestra-containing food would not alter the amount of vitamin 
available for absorption (61 FR 3118 at 3144-3147). The amounts of the 
vitamins to be provided are prescribed to ensure safe use (Sec.  
172.867(d)). As required under section 403(i) of the act, these 
vitamins are declared in the ingredient listing.
    The added vitamins were not to be considered in determining 
nutrient content of the food for the nutritional label or for any 
nutrient claims, expressed or implied. This is because the added 
vitamins simply compensate for the transient impaired absorption of 
vitamins A, D, E, and K, i.e., they are added to ensure no change 
(neither increase nor decrease) in vitamin availability. Thus, the 
vitamins added to olestra do not contribute significant amounts of 
these nutrients to the diet (61 FR 3118 at 3161).
    Labeling may be considered misleading not only if it fails to 
reveal facts that are material in light of consequences that may result 
from use of a food, but also if the labeling fails to reveal facts that 
are material in light of representations made. Therefore, to set the 
context for why vitamins A, D, E, and K were added, FDA required a 
label statement providing information both that vitamins A, D, E, and K 
had been added and that olestra inhibits the absorption of vitamins. 
Because FDA believed that consumers who see vitamins A, D, E, and K in 
the ingredient listing might incorrectly believe that the food was 
fortified with these vitamins, the agency required an explanatory 
statement on the label of olestra-containing foods to inform consumers 
that olestra-containing foods were not an enhanced source of vitamins 
A, D, E, and K. The statement indicated that olestra inhibits the 
absorption of vitamins and other nutrients to explain why they were 
added. FDA included the term ``other nutrients'' because any nutrient 
that is as lipophilic as these vitamins would also be affected, 
although FDA concluded that there was no basis for adding back 
nutrients other than vitamins A, D, E, and K. In this way, FDA sought 
to make clear to consumers the reason for the presence of vitamins A, 
D, E, and K in the ingredient listing.
    Carotenoids are fat-soluble components in the diet, the majority of 
which are derived from fruits and vegetables. Data from the 
petitioner's two 8-week studies demonstrated that consumption of 
olestra inhibits absorption of carotenoids as measured by a decrease in 
serum carotenoid levels (61 FR 3118 at 3147-3149). Co-consumption of 
olestra and a carotenoid-containing food allows the greatest 
interaction between olestra and the carotenoid, thereby maximizing the 
potential for interfering with absorption of the carotenoid from the GI 
tract.
    Beta-carotene is a provitamin A carotenoid that is a dietary source 
of vitamin A; provitamin A carotenoids are converted in the body into 
vitamin A. At the time of the 1996 final rule, FDA concluded that 
supplementing olestra-containing foods with vitamin A would compensate 
for olestra's effects on the provitamin A function of carotenoids.
    In evaluating whether there is a scientific basis to require the 
addition of any carotenoids to olestra-containing foods, FDA consulted 
with scientists at the National Cancer Institute of the National 
Institutes of Health (NIH) and the National Eye Institute (NEI) of the 
NIH (61 FR 3118 at 3148-3149), and the agency's Food Advisory Committee 
(FAC) (61 FR 3118 at 3121). At the 1995 FAC meeting on olestra, experts 
with a range of views discussed whether carotenoids themselves have 
beneficial health effects, or whether it is some other substance in 
fruits and vegetables that provides the claimed health effects, in 
which case the carotenoids are serving solely as markers for fruit and 
vegetable consumption. Five different conferences or reviewing groups 
preceding the 1995 FAC meeting had examined the relationship between 
carotenoids and disease. All of these groups had concluded that there 
was insufficient evidence to recommend consumption of carotenoids, 
except to encourage the consumption of fruits and vegetables (61 FR 
3118 at 3148). Although epidemiological studies showed an association 
between diets rich in fruits and vegetables (including those that 
contain carotenoids) and decreased cancer risk, there was no direct 
evidence that carotenoids themselves were responsible for or 
contributed in a significant way to that protective benefit. Therefore, 
at the time of the approval of olestra, the agency
 
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concluded that the available data did not establish any identifiable 
nutritional or prophylactic benefits for carotenoids, either 
individually or collectively, aside from the provitamin A function (61 
FR 3118 at 3147-3149).
    Thus, FDA found no scientific basis for requiring the addition of 
any carotenoid to olestra-containing foods. The agency also found that 
the actual magnitude of olestra's effects on carotenoid absorption was 
likely to be within the range of the normal variation of such 
absorption due to diet and bioavailability, providing additional 
assurance that the effect of olestra on the absorption of carotenoids 
did not raise concern. Accordingly, FDA concluded that there was no 
basis for requiring a statement about carotenoids on the label of 
olestra-containing food.
 
B. Opportunity for Comment and Consideration of New Data
 
1. Request for Comments on the Label Statement Required by the 1996 
Final Rule
    Because section 409 of the act prohibits, among other things, 
approval of a food additive if doing so would cause misbranding, the 
agency concluded that the olestra label statement should be imposed as 
a requirement as part of the food additive petition process (Sec.  
172.867(e)). The agency acknowledged, however, that the specific 
wording had not been tested or subject to an opportunity for comment. 
Thus, the agency requested comments on the label statement from 
interested persons on such issues as the need for labeling, the 
adequacy of its content, and the agency's current word choices (61 FR 
3118 at 3160).
    After the publication of the 1996 final rule, the agency received 
timely comments on the label statement,\4\ as well as objections to the 
1996 final rule.\5\
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    \4\ The comments received by April 1, 1996, included the results 
of P&G's consumer focus group studies on the label statement. Frito-
Lay also submitted consumer perception studies on the olestra label 
statement. These studies are discussed in section III.F.1 of this 
document. The agency continued to receive comments on the label 
statement after April 1, 1996. In this document, FDA addresses 
comments received on the label statement regardless of whether the 
comments were received by April 1, 1996.
    \5\ Timely objections were to be filed by February 29, 1996. 
FDA's response to these objections and requests for hearing is 
published elsewhere in this issue of the Federal Register.
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2. P&G's Commitment To Further Studies
    In a letter to the agency dated January 24, 1996, the petitioner 
stated its intention to conduct focus group testing of the required 
olestra label statement, to establish a postmarket surveillance system, 
to conduct additional studies of olestra exposure (both amounts 
consumed and patterns of consumption), and to conduct additional 
studies regarding the effects of olestra consumption (61 FR 3118 at 
3160 and 3168). FDA responded that P&G was to conduct the studies it 
had identified in its letter to FDA, consistent with the timetables 
identified in that letter (61 FR 3118 at 3168).
    P&G did carry out the surveillance and studies outlined in its 
letter of commitment, and performed additional studies not mentioned in 
the January 1996 letter. After the publication of the 1996 final rule, 
P&G carried out its commitment to establish a system of passive 
surveillance to collect spontaneous reports of possible effects that 
consumers associated with the consumption of olestra-containing snacks. 
This system included establishing an outside panel of medical experts 
to review reports, followup on reports of serious illness, and provide 
FDA information about reports received.
    P&G also carried out its commitment to conduct studies on the 
exposure and effects of olestra. The active surveillance program that 
P&G sponsored was designed to examine the impact of olestra consumption 
on endpoints such as serum concentrations of carotenoids and vitamins, 
olestra consumption patterns (including frequency and amounts), and GI 
symptoms.
    These data and information were presented to the FAC in June 1998, 
and were eventually incorporated into the petition that is the subject 
of this rulemaking.
3. FDA's Commitment To Convene an FAC Meeting
    In the 1996 final rule, FDA committed to review and evaluate any 
new data and information bearing on the safety of olestra and to 
present such information to the agency's FAC within 30 months of the 
approval of the use of olestra in savory snacks (61 FR 3118 at 3168-
3169; Sec.  172.867(f)).
    FDA convened a meeting of its FAC within 30 months of the approval 
of the use of olestra in savory snacks. At an open public meeting, held 
June 15-17, 1998, new data and information concerning olestra, obtained 
since the 1996 approval were presented (Ref. 1). These new data, which 
comprise the majority of material that P&G subsequently submitted in 
its petition, are discussed in section III of this document. FDA, P&G, 
the Center for Science in the Public Interest (CSPI), and other 
interested members of the public made presentations to the Committee. 
After presentation of the new data, the FAC discussed the label 
statement specified in Sec.  172.867(e). The complete set of 
transcripts of the June 1998 FAC meeting (``the transcript'' or 
``transcript'') is publicly available through FDA's Division of Dockets 
Management and through FDA's Internet site.\6\
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    \6\ The Internet site is located at http://www.fda.gov/ohrms/dockets/ac/cfsan98t.htm#Food
 
 Advisory Committee (choose June 15, 16, 
and 17).
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4. P&G's Petition To Remove the Requirement for the Label Statement
    P&G submitted a food additive petition, dated December 1, 1999, to 
amend the food additive regulations in Sec.  172.867 Olestra by 
removing the requirement for the label statement prescribed in Sec.  
172.867(e). This petition incorporated the studies and information that 
were performed after the publication of the 1996 final rule. As noted, 
much of that material was discussed by the FAC in 1998.
5. Comments Received
    FDA received approximately 80 letters, each containing one or more 
comments, on the olestra label statement.\7\ \8\ Some of the comments 
were submitted in response to FDA's request in the 1996 final rule for 
comments on the olestra label statement. Other comments were submitted 
in response to the January 24, 1996, announcement of the approval of 
olestra for use in savory snacks. Because all of these comments 
addressed P&G's original petition, which was granted in 1996, in this 
document FDA refers to these comments as comments ``to the 1996 final 
rule.'' Comments were also submitted in response to publication in the 
Federal Register of the filing notice for the current petition (65 FR 
11585, March 3, 2000); in this document, FDA refers to these comments 
as comments ``to the current petition.''
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    \7\ FDA notes that one of the objections submitted by CSPI 
concerns the label statement required by the 1996 final rule.
    \8\ Although not part of the petition being considered in the 
current rulemaking, FDA reviewed comments regarding labeling that 
were addressed to the 1998 FAC. These comments raised no substantive 
issue that was not already considered as part of the current food 
additive petition.
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    Comments were submitted by P&G, Frito-Lay, Inc. (Frito-Lay), and 
other members of the food industry, as well as from individual 
consumers, consumer organizations, academia, trade associations, and a 
member of Congress. Several comments were filed by CSPI. Several 
parties, including Frito-Lay and
 
[[Page 46368]]
 
CSPI, submitted comments to both the 1996 final rule and the current 
petition.
    Although section 409 of the act establishes no comment period for 
food additive petitions, and the agency generally does not solicit 
comments in notices announcing the filing of a food additive petition, 
it is FDA's practice to consider any relevant comments submitted prior 
to the agency's decision on a petition.\9\ In this document, FDA 
separately discusses data from telephone surveys and passive 
surveillance regarding GI effects, new studies regarding GI effects, 
and active surveillance and other information regarding nutritional 
effects of olestra. As part of its discussion of these areas, FDA 
describes and responds to comments relevant to the topic. FDA discusses 
and responds to comments on other topics (such as the wording of the 
label statement, the prominence and placement of the label statement, 
and the need for a label statement) in a separate section (see section 
V of this document). In responding to the submitted comments, FDA has 
considered all of the data and information available in the record that 
bear on the olestra label statement, including the data and information 
in the 1996 final rule as well as the new information in the current 
petition.
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    \9\ See discussion of comments in the filing notice for this 
petition (65 FR 11585-11586, March 3, 2000).
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III. Data and Information Since the 1996 Final Rule
 
A. Introduction
 
    Olestra-containing snacks were introduced into test markets in 
April 1996, and national marketing began in February 1998. P&G 
established a system of passive surveillance to collect reports of 
possible effects that consumers associated with eating olestra-
containing snacks. This surveillance system was in place when test 
marketing began. P&G has submitted reports to the agency, as well as 
analyses of such reports. P&G also established its program for active 
surveillance to monitor, among other things, possible nutritional 
impacts of olestra consumption.
    P&G conducted studies concerning possible GI effects from consuming 
olestra-containing snacks in ``real-life'' situations. Specifically, 
P&G conducted four controlled studies concerning possible GI effects in 
humans and submitted reports about those studies to FDA.\10\ The four 
controlled studies are described as follows:
---------------------------------------------------------------------------
 
    \10\ A copy of the petition submitted by P&G, as well as copies 
of the studies, surveys, and other supporting materials listed here, 
can be found at the Division of Dockets Management, Docket No. 00F-
0792.
---------------------------------------------------------------------------
 
    [sbull] An Acute Consumption Study,
    [sbull] A Six-Week Consumption Facilitated Ad Lib Study (also 
called the Home Consumption Study),
    [sbull] A Rechallenge Study, and
    [sbull] A Stool Composition Study.
    In the current petition, P&G also submitted the following data and 
information:
    [sbull] Reports and analyses of data collected through consumer 
focus group and perception studies,
    [sbull] Surveys regarding GI symptoms,
    [sbull] Updated literature reviews on carotenoids and disease, and
    [sbull] A report and analysis of the first year of data collected 
in an Active Surveillance Study.
    CSPI also submitted reports from individuals who attributed an 
effect to the consumption of an olestra-containing food (Docket No. 
87F-0179). In some cases, CSPI obtained medical records from consumers 
and forwarded them to FDA for analysis.
    Below, FDA describes in detail the studies and information 
submitted in support of this petition, comments to the 1996 final rule 
that discuss the labeling of olestra-containing foods, comments to the 
current petition, and other relevant information.
 
B. Surveys and Postmarket Passive Surveillance Regarding GI Effects
 
1. Telephone Surveys Regarding GI Complaints
    a. P&G. P&G sponsored two telephone surveys to investigate the 
frequency and severity of GI complaints, to investigate the frequency 
of consumption of foods that consumers believe cause GI symptoms, and 
to determine knowledge about reported GI symptoms from olestra-
containing foods. Both of these surveys were performed before olestra-
containing foods were available for sale in those markets. The first 
survey was done in February 1997 in Indiana (in Marion County, where 
Indianapolis is located), which was later a test-market for olestra-
containing foods. This survey also served as a pilot study for the 
second survey, which was a national survey of the U.S. population 
completed in September 1997. National marketing of olestra-containing 
foods began in February 1998.
    The petitioner acknowledged limitations in the design of the first 
survey completed in Indiana. For example, because the first survey was 
also the pilot study, the study instrument had not yet been 
validated.\11\ Also, the sample size was small and not shown to be 
representative of the general population surveyed. Despite these 
limitations, the petitioner concluded from the survey that GI symptoms 
were very common among the adult respondents polled. Asked about the 
previous three month period, respondents reported most frequently the 
GI symptoms of gas (34.6 percent), diarrhea (33.2 percent), and 
abdominal cramps (25.8 percent). Of those respondents who experienced 
one or more GI symptoms, 14 percent reported seeking medical attention 
because of the symptom. More than half of those who experienced a GI 
symptom said it was of moderate to severe intensity. The other result 
noted by the petitioner in this study was that there are a number of 
common foods (e.g., beans, onions, spicy foods) that respondents said 
caused them to have GI symptoms, but more than 80 percent of these 
respondents said they continued to eat these foods. Approximately half 
of the respondents had heard of olestra and among that group, 18 to 28 
percent associated olestra with a GI symptom such as abdominal cramping 
or diarrhea.
---------------------------------------------------------------------------
 
    \11\ Data obtained from the first survey was used to validate 
the study instrument for use in the second survey.
---------------------------------------------------------------------------
 
    The second survey was a larger, national survey that was designed 
with a reliability check, and a portion of the survey was designed to 
be a truly random sample of respondents. In this survey, 40.5 percent 
of respondents reported having one or more GI symptoms in the previous 
month. Of those respondents reporting a GI symptom, 21.8 percent had 
abdominal pain or discomfort, and 26.9 percent reported diarrhea or 
loose stools. More than 65 percent of respondents rated each of their 
symptoms as moderate to severe in intensity, and 14 percent consulted 
physicians about their symptoms. When asked about specific foods, 
respondents reported having GI symptoms after eating foods such as 
beans (22 percent) or spicy foods (34.4 percent). Despite symptoms, 
approximately 80 percent continued to consume these foods. The 
petitioner also found that women were more likely than men to report GI 
symptoms, and that abdominal pain, discomfort, and bloating were more 
commonly reported by women. There was little difference between males 
and females for reports of diarrhea. More than half the respondents in 
this study had heard of olestra, and of those, a varying number 
associated olestra with different GI
 
[[Page 46369]]
 
symptoms (diarrhea (33 percent), loose stools (4 percent), cramps (11 
percent), other GI problems (23 percent)).
    FDA notes that in both these surveys, the percent of individuals 
reporting a GI symptom was high. FDA also notes that while the great 
majority of respondents in both surveys indicated that they consumed 
foods that caused them GI symptoms, the survey did not obtain 
information about the severity of these symptoms (Ref. 2).
    b. CSPI. In 1996, CSPI commissioned a telephone survey in cities 
where olestra-containing foods were test marketed (Cedar Rapids, IA, 
Eau Claire, WI, and Grand Junction, CO), and submitted a report of the 
results to FDA.\12\ The purpose of CSPI's survey was to determine how 
many people in the test market had tried olestra-containing snacks, and 
of those who had eaten olestra-containing snacks, how many had 
experienced GI symptoms. A random digit dialing sampling system was 
used, until a total of 506 telephone interviews were conducted in June 
and July 1996. CSPI said that 27 percent of individuals surveyed had 
tried the newly marketed olestra-containing chips, and of those, 20 
percent reported experiencing GI symptoms characterized by CSPI as an 
adverse GI effect. Respondents characterized these events as mild (58 
percent), moderate (23 percent), or severe (9 percent). CSPI also found 
that the majority of respondents (78 percent) had seen negative reports 
in the press about olestra, although only 28 percent said they were 
concerned about these possible effects. Based on this telephone survey, 
CSPI predicted that a large number of adverse events would be caused by 
the national marketing of olestra-containing foods. CSPI performed a 
separate survey of the original respondents who had not eaten olestra-
containing chips but ate other chips to assess the frequency of GI 
events associated with consumption of conventional savory snacks and 
found that only 0.5 percent associated an adverse GI effect with eating 
a triglyceride savory snack.
---------------------------------------------------------------------------
 
    \12\ CSPI submitted this report to Docket No. 87F-0179.
---------------------------------------------------------------------------
 
    CSPI commissioned a second survey, which was conducted in April and 
May 1997 in the Indianapolis area where olestra-containing foods were 
test-marketed. The purpose of the survey was to ascertain the 
consumption of olestra-containing foods and possible rate of adverse 
effects. CSPI submitted a report of the results to FDA.\13\ CSPI 
reported that the majority of respondents said they had eaten savory 
snacks in the past 8 weeks (68.8 percent), and that a smaller portion 
of respondents (32.7 percent) said they had eaten olestra-containing 
foods. CSPI said that when respondents were asked whether they had 
eaten a specific brand of chips that contain olestra, they said yes, 
but when asked whether they had eaten olestra, these consumers 
responded that they had not eaten olestra. Of the group of respondents 
who had eaten an olestra-containing food, 8.3 percent reported 
experiencing what was characterized as an adverse effect after eating 
the olestra-containing food.
---------------------------------------------------------------------------
 
    \13\ CSPI submitted this report to the Docket No. 87F-0179.
---------------------------------------------------------------------------
 
    In its review of the data and information submitted by CSPI, FDA 
found that the studies provided information about the prevalence of use 
of olestra-containing foods, awareness of GI symptoms associated with 
olestra, and sources of information that consumers were using to learn 
about GI symptoms associated with olestra. FDA disagreed, however, that 
these studies could provide information about the cause of these GI 
symptoms. FDA found that the study design was inadequate to determine 
the cause of GI symptoms. Additionally, it is known from food-borne 
illness outbreaks that attribution biases can influence consumers and 
lead to the erroneous attribution of symptoms to a particular food. 
CSPI's survey does not allow for the evaluation of erroneous 
attribution of GI symptoms to consumption of olestra-containing chips, 
i.e., other plausible causes for illness reports were not considered 
(Ref. 3).
2. Postmarket Passive Surveillance by P&G
 
    P&G established a system of passive surveillance to collect 
consumer reports associated with the consumption of olestra-containing 
foods. Passive surveillance refers to the collecting of spontaneous, 
voluntary reports about a product. In its petition, P&G presents an 
overview of both the utility and limitations of data obtained from 
spontaneous, postmarket consumer reports. P&G characterized postmarket 
passive surveillance as a means of identifying and characterizing 
potential issues, including safety issues, once a product has entered 
the marketplace and been utilized by the population at large. The 
population experience with a product will be much broader than that 
derived during premarket testing because the number of individuals 
participating in premarket testing is necessarily limited. A reporting 
rate may be calculated based on the total amount of product sold and 
the number of reports received. P&G notes, however, that there are a 
number of limitations with passive surveillance reporting. For example, 
these data do not lend themselves to assessment of causality because of 
the lack of controlled conditions and various confounding factors, such 
as a high background incidence of reported GI effects. Voluntary 
reporting, such as that obtained in P&G's passive surveillance system, 
is also subject to a number of biases including the level of attention 
the subject is receiving in the news media. Because reporting is 
voluntary and subject to interpretation, and because the total number 
of ``exposures'' can only be estimated, a true incidence rate cannot be 
calculated from passive surveillance.
    Reports to P&G under its passive surveillance program for olestra 
were, for the most part, collected via calls made by consumers to a 
toll-free telephone number displayed on olestra-containing foods. Such 
calls were taken directly by P&G via its own toll-free telephone 
number. Calls were also forwarded to P&G by other snack food 
manufacturers (specifically, Frito-Lay). In some cases, information 
from such calls (but not the calls themselves) was forwarded to P&G by 
other snack manufacturers. Information was collected from callers as to 
the product used, specific product code information (where available), 
amount consumed, the nature of the complaint, symptom onset and 
duration, recurrence, characteristics and treatment, concomitant 
medications, and physician or other health professional involvement. 
Where physician contact was involved, or a medically significant event 
was reported, the petitioner attempted to obtain more detailed 
information including release of medical records for evaluation.
    Consumer reports were reviewed by trained medical affairs staff at 
P&G. Additionally, the petitioner established a committee (Olestra 
Postmarketing Surveillance Committee) of medical experts outside of P&G 
 
whose membership included specialists in GI disease (both adult and 
pediatric GI), epidemiology, and pharmacology to review the reports 
received, and to make recommendations about the implications, if any, 
of these reports on the safety of olestra. The petitioner submitted 
reports to FDA of complaints associated with olestra consumption 
beginning in April 1996 with the test marketing of snacks made with 
olestra.
    The petitioner reported that there were peaks in the number of 
reports received after the test marketing and
 
[[Page 46370]]
 
national introduction of olestra-containing foods. The petitioner found 
that while the absolute number of reports increased when olestra-
containing foods were first introduced into test markets, the reporting 
rate (reports per amount of product sold) declined over time. The 
petitioner also found that over time the absolute number of reports 
declined and eventually reached a plateau. The greatest number of 
reports the petitioner received over a four month period was 4,951 in 
1998 at the national introduction of olestra-containing snacks. The 
petitioner stated in its initial reports on passive surveillance that 
it is common to receive calls and complaints for products. At the start 
of national marketing the reporting rate was one report for 
approximately 100,000 servings sold, and 2 years later the reporting 
rate was one report for approximately 1 million servings sold.
    The petitioner analyzed the data from its passive surveillance 
efforts and found no trend toward increased symptoms with increased 
consumption; no trend towards increased severity with increased 
consumption; and no difference in severity by age group or gender. The 
petitioner's Olestra Postmarketing Surveillance Committee reviewed 
reports using an algorithm developed to assess the likelihood that an 
effect was caused by olestra. Using this algorithm, P&G's committee 
concluded that many reports were not likely to be related to olestra 
and no serious reports could be attributed to olestra (Docket No. 00F-
0792, submission dated March 3, 2000). Based on the nature of the 
complaints received, the petitioner designed subsequent studies to 
address, in part, issues arising from consumers' anecdotal reports 
after eating olestra-containing foods.
    In the 1996 final rule, FDA determined that the use of olestra was 
safe based on results from the preapproval safety studies. FDA stated 
in the 1996 final rule (61 FR 3118 at 3168) that P&G's plans to 
continue to study the consumption and effects of olestra were both 
prudent and responsible. FDA expected, based on results of the 
preapproval studies, that some reports concerning GI upset, such as 
loose stools and abdominal cramping, would be collected through a 
system of passive surveillance. FDA also considered that postmarket 
passive surveillance had the potential to detect low frequency and 
unexpected events because postmarket passive surveillance involves the 
entire population that consumes a product.
    FDA reviewed the reports of effects attributed to olestra and found 
that the majority of reports received concern GI effects such as loose 
stools and abdominal cramping. Other symptoms were reported at lower 
frequencies.
    FDA recognizes that passive surveillance data such as those 
collected by P&G have utility but are limited in that they do not allow 
for the determination of a causal association between the product 
consumed (i.e., olestra-containing foods) and effects reported. Such 
reports can, however, lead to hypothesis generation about why specific 
effects are occurring. This may then result in the development of 
studies used to test these hypotheses (Ref. 4).
    FDA reviewed reports of effects associated with ingestion of 
olestra that led consumers to seek medical attention. Where possible, 
the agency reviewed medical records that were obtained directly from 
individuals who reported the effect or that were obtained through P&G 
and CSPI (Refs. 5 and 6). At the 1998 FAC meeting, FDA presented its 
analysis of the medical reports received up to that time. Among the 
reports discussed was a case where a consumer had undergone an 
appendectomy and associated this with consuming an olestra-containing 
food. The pathology diagnosis at the hospital noted that there were 
minimal inflammatory changes. FDA obtained a medical release from the 
patient in order to examine the pathology slides from the appendectomy, 
which were read independently by four FDA pathologists, all of whom 
confirmed the presence of inflammatory cells throughout the wall of the 
appendix meriting a diagnosis of acute appendicitis.\14\ In many other 
of the medical records reviewed, physicians attributed patient symptoms 
to an etiology other than olestra, or did not provide an etiology. 
There were cases where physicians did attribute symptoms to olestra, 
but the limitations of passive surveillance make it difficult, if not 
impossible, to draw definitive conclusions about causality based on the 
review of individual medical records.
---------------------------------------------------------------------------
 
    \14\ Transcript, vol. 1, pp. 271-276.
---------------------------------------------------------------------------
 
3. Postmarket Surveillance Reports From CSPI
    CSPI has periodically submitted to FDA reports of effects allegedly 
associated with the consumption of olestra (Docket No. 87F-0179). The 
complaints were gathered initially in test markets by calls to an 
advertised toll-free telephone line, and gathered subsequently through 
CSPI's Internet site.
    FDA analyzed the reports from CSPI and compared the information and 
analysis to the information and analysis of the reports submitted to 
FDA by P&G. FDA noted that the reports received by CSPI were very 
similar in nature, type of complaint, and amount consumed as the 
reports by P&G.\15\ As discussed previously, passive surveillance has 
limited utility in determining causality.
---------------------------------------------------------------------------
 
    \15\ Transcript, vol. 1, pp. 258-270.
---------------------------------------------------------------------------
 
4. Comments Regarding Consumer Reports
    FDA received comments about reports of effects that consumers 
attributed to olestra. FDA considered these comments and responds in 
the following section of this document.
    (Comment 1) One comment from an individual consumer to the current 
petition reported that a family member who had Addison's disease 
suffered gastric cramps and diarrhea, laid down, went into an 
Addisonian crisis, and died after consuming olestra-containing potato 
chips. The comment did not provide any further information regarding 
the death mentioned. CSPI forwarded to the agency the medical record of 
an Addison's disease patient who had reportedly consumed olestra-
containing potato chips prior to death. The patient who died was 
diagnosed as having Addison's disease (adrenocortical insufficiency) 
and hypothyroidism in 1989. FDA believes, based on several factors, 
that the comment and medical record provided by CSPI refer to the same 
person.
    FDA reviewed the medical record forwarded by CSPI. This patient 
collapsed suddenly after experiencing a bout of gastroenteritis, and 
reportedly consumed olestra-containing chips prior to the bout of 
gastroenteritis. An autopsy showed that the adrenal glands could not be 
identified and noted a finding of Hashimoto's thyroiditis. The medical 
record did not provide any information regarding the gastroenteritis 
experienced prior to death.\16\ Due to the lack of information 
contained in the medical record, the agency was unable to determine 
whether the ingestion of olestra had any role in this patient's illness 
or death (Ref. 5).\17\
---------------------------------------------------------------------------
 
    \16\ The Certificate of Death lists acute cardiorespiratory 
arrest as the immediate cause of death with autoimmune 
adrenocortical deficiency syndrome as the underlying cause leading 
to the immediate cause of death. Other significant conditions 
contributing to death but not resulting in the underlying cause 
include mitral valve prolapse and Hashimoto's thyroiditis.
    \17\ FDA investigated the death mentioned in the comment. As 
part of the investigation, FDA spoke with the patient's spouse and 
the patient's co-workers about the events leading up to the 
patient's death.
 
---------------------------------------------------------------------------
 
[[Page 46371]]
 
    (Comment 2) A comment from CSPI to the current petition asserted 
that FDA has never conducted indepth investigations (beyond reviewing 
the medical records of a few individuals) of any of the anecdotal 
reports, including those reports involving rectal bleeding, 
hospitalization, and death. The comment further asserted that the 
agency has ignored all of the anecdotal reports and has said that there 
is no proof that any of the reports were due to olestra. The comment 
also stated that in some reports, a patient's physician attributed his/
her symptoms to olestra. The comment also quoted FDA review memoranda 
(Refs. 6 and 7) stating that olestra may have been responsible for some 
of the effects reported.
    FDA does not agree that it has ignored anecdotal reports. Nor does 
it agree that it must conduct further investigation of the anecdotal 
reports. FDA regularly reviews the reports forwarded to the agency by 
P&G and CSPI. The reports are analyzed and summarized using criteria 
such as sex, age, symptoms reported, duration of symptoms, and amount 
of olestra-containing food consumed. The agency also reviews any 
medical records forwarded with the reports. CSPI provided no evidence 
to support its allegation that anecdotal reports have been ignored. Nor 
has CSPI provided any reason to suspect that serious adverse health 
effects could have been caused by olestra. The agency will continue to 
monitor reports as they are forwarded to the agency.
    As stated in the memoranda cited by the comment, some of the 
effects reported may have been caused by olestra. These reports were 
collected using passive surveillance. As noted previously, passive 
surveillance is useful in that it can lead to hypothesis generation 
about why specific effects are occurring. These hypotheses can then be 
tested in controlled clinical trials. For example, the reports received 
from consumers attributing their symptoms to olestra served as a basis 
for some of the hypotheses tested in the petitioner's most recent 
controlled clinical studies. However, while passive surveillance data 
have utility, such data are limited in that they do not allow for the 
determination of a causal association between the product consumed and 
effects reported. Thus, based on the passive surveillance data alone, 
it is not possible to determine whether the effects reported were 
caused by consumption of an olestra-containing food.
    The agency has reviewed all of the medical records that it has 
received from CSPI and P&G about consumers who saw a physician for an 
effect attributed to the consumption of an olestra-containing food. In 
fact, FDA has conducted an investigation into the death mentioned in 
the previous comment. FDA has also obtained and examined the pathology 
slides of a patient who had undergone an appendectomy that the patient 
associated with consumption of an olestra-containing food. The agency 
has not found sufficient evidence to conclude that olestra is likely to 
have caused the symptoms that led the consumers to see a physician.\18\
---------------------------------------------------------------------------
 
    \18\ Ref. 5 and Transcript, vol. 1, pp. 271-276.
---------------------------------------------------------------------------
 
    (Comment 3) A comment from CSPI to the current petition stated that 
letters and electronic mail messages sent to P&G describing GI symptoms 
have not been included in reports that P&G submitted to the agency; 
therefore, the agency has not received all of the symptom-related 
reports. The comment recommended that the agency investigate whether it 
had received all reports.
    FDA recognizes that not every report from a consumer will provide 
enough information for FDA to determine whether an effect was possibly 
related to olestra and that some judgement is needed in compiling data. 
In light of this limitation, the agency recognizes that P&G may not 
forward all reports it receives, such as those reports containing 
incomplete information, to the agency. While this may mean that less 
than 100 percent of reports are collected, the agency has no reason to 
believe that the complaints not forwarded to the agency constitute a 
unique data set or raise an issue not previously considered. Indeed, 
the reports gathered and forwarded independently to the agency by P&G 
 
and CSPI are consistent in terms of the nature of the complaints and 
the amounts of olestra consumed. CSPI's comment provides no specific 
information that would lead the agency to conclude that it has not 
received an accurate and representative sample of the effects reported 
to P&G or that such reports raise an issue not already considered. 
Thus, the agency finds that there is no basis for concluding that it 
should obtain and evaluate each and every report that P&G receives.
    (Comment 4) A comment from CSPI to the current petition stated that 
the agency should obtain and disclose to the public the number of 
consumers (without identifying any particular individuals) who 
attributed their symptoms to olestra and reached an out-of-court 
settlement with the petitioner. The comment also asked for the number 
of consumers who, after attributing their symptoms to olestra, received 
or were offered reimbursement for their medical expenses. The comment 
requested that the agency consider this information in its rulemaking.
    FDA does not agree that it should obtain and disclose to the public 
the number of consumers who attributed their symptoms to olestra and 
reached an out-of-court settlement with the petitioner. Importantly, 
the comment does not demonstrate the relevance of the requested 
information to the question at issue: i.e., whether FDA should continue 
to require special labeling for olestra-containing foods. Moreover, 
settlement of lawsuits may be reached for a variety of reasons, 
including improved public relations or avoidance of unnecessary 
conflict, and do not address any factual issues regarding whether 
olestra is capable of causing the effects claimed.
 
C. Studies Regarding GI Effects
 
1. Rechallenge Study
    The petitioner submitted a report of a study designed to test 
whether individuals who complained of a GI effect after consuming 
olestra-containing snacks would have the same experience with 
subsequent exposure (Refs. 8 and 9). This test was designed to show 
whether the GI effect is consistently associated with consumption of 
the olestra-containing snack. The petitioner's study was a randomized, 
double-blind, placebo-controlled, four-period, within-subject crossover 
study. Subjects were recruited from consumers who had voluntarily 
called the snack manufacturer and reported GI symptoms associated with 
consumption of olestra-containing snacks. Each subject made four visits 
to the study site, at least 1 week apart, and was provided with 2 
ounces (oz) of either potato chips containing olestra (olestra chips) 
or potato chips containing conventional triglyceride \19\ (triglyceride 
chips). At each visit, subjects were to consume as much as they could 
of the 2 oz serving. Each participant was randomly assigned to receive 
olestra chips at two visits and triglyceride chips at two visits. 
Participants were contacted after each visit and asked whether they had
 
[[Page 46372]]
 
experienced any GI symptoms within the week after eating the potato 
chip product.
---------------------------------------------------------------------------
 
    \19\ In the various reports submitted by the petitioner, the 
terms triglyceride, full-fat, regular, and conventional were all 
used to describe the oil used in savory snacks. These terms mean the 
same thing. For consistency in this document, we use the word 
triglyceride.
---------------------------------------------------------------------------
 
    The study was completed with 98 participants, the majority of whom 
had initially called to report that they had experienced diarrhea, 
loose stools, and/or abdominal cramping (61 percent, 16 percent, and 64 
percent respectively). Approximately 48 percent of the participants 
described the symptoms that prompted their original call as severe. For 
nearly three-quarters of the participants, the amount of olestra chips 
consumed in the study was comparable to, or greater than, the amount 
associated with their initial call.
    The petitioner found that during the study there were no 
significant differences following consumption of olestra chips, 
compared with consumption of triglyceride chips, in the frequencies of 
abdominal cramping (12 percent with olestra, 9 percent with 
triglyceride), diarrhea or loose stools (11 percent with olestra, 15 
percent with triglyceride), gas (7 percent with olestra, 5 percent with 
triglyceride), or any other GI symptom (28 percent with olestra, 26 
percent with triglyceride). Overall symptom severity ratings for all 
subjects were similar after consumption of olestra and triglyceride 
chips. The petitioner concluded that this study provided evidence that 
an episode that was initially reported to be an olestra-related effect 
was in all likelihood not olestra-related, and that there was no 
evidence of a population or subpopulation with a sensitivity to 
olestra. The petitioner suggested that these results indicate that 
initial calls made to the toll-free telephone line may reflect false 
attribution of symptoms to products made with olestra.
    FDA found this study was adequately representative of the 
population who called the postmarketing surveillance system in terms of 
severity of initial symptoms and amount of olestra reportedly consumed 
prior to the initial symptom episode. FDA noted that while 98 
participants were enrolled in the study, only 92 completed all 4 
visits. The six dropouts were unrelated to olestra-related effects. 
Based on an analysis of the data in the study, FDA concluded that under 
the conditions of the study (two exposures of up to 2 oz of olestra-
containing chips separated by at least a week), subjects eating 
olestra-containing chips were no more likely to report having had loose 
stools, abdominal cramps, or any other GI symptom compared to subjects 
eating an equivalent amount of triglyceride chips (Refs. 10 and 11).
2. Acute Consumption Study
    P&G sponsored \20\ a study to determine whether there was a 
difference in the nature or frequency of GI symptoms experienced by 
subjects eating olestra chips compared to those eating triglyceride 
chips, ad libitum on a single eating occasion (Ref. 12). The study was 
a randomized, placebo-controlled, double-blind study in which 1,092 
adults and teenagers who were provided with a 13 oz bag of potato chips 
(either olestra chips or triglyceride chips) in a plain, unlabeled 
white bag, consumed as many chips as they desired while viewing a 
movie. Participants were also provided a 32-oz soft drink of their 
choice. Participants were told prior to the test that they might 
experience temporary dry mouth, thirstiness, or digestive symptoms 
(such as gas, cramping, or loose stools), as they might with salty or 
high fiber foods.
---------------------------------------------------------------------------
 
    \20\ The principal investigator for the study was Dr. L. 
Cheskin, Dept. of Gastroenterology, Johns Hopkins School of 
Medicine.
---------------------------------------------------------------------------
 
    Participants were instructed to be seated in the theater at least 
one seat apart from other participants, to eat and drink as much or as 
little of their chips and beverage as they desired, and not to share 
with anyone else. The theaters were monitored by several study staff 
during the movies. At the conclusion of the movie, participants clipped 
their bags of chips shut; noted the approximate amount of beverage 
consumed; and completed a brief questionnaire about product acceptance, 
satiety, and sensory attributes. Participants turned in the completed 
questionnaires and bags with uneaten chips and were given a toll-free 
telephone number to call if they had any questions or problems. Bags of 
chips were subsequently weighed to determine the amount consumed by 
each subject.
    Trained telephone interviewers contacted study participants and 
administered a recall questionnaire to collect information on any 
effect experienced since the movie. All subjects were specifically 
asked if they had experienced any GI symptoms during or since the 
movie, and to specify those symptoms including the severity and timing 
of any such symptoms. The study protocol specified that participants be 
contacted within 2 to 4 days of viewing the movie. The petitioner 
reported that 85 percent were contacted within 2 to 4 days and a total 
of 97 percent were contacted within a week of viewing the movie.
    The petitioner reported that the median consumption of olestra 
chips was approximately 2.1 oz (approximately 16 g of olestra) \21\ 
compared to about 2.7 oz of triglyceride chips. Overall chip 
consumption was similar across age groups, but males generally consumed 
more chips than females (median of 2.8 versus 2.1 oz, p<0.01). The 
overall palatability of the triglyceride chips was rated slightly 
higher than the olestra chips, with a mean score of 6.4 versus 5.6 on a 
9-point preference scale (p<0.01). Regarding satiety, there were no 
significant differences between the groups as indicated by mean satiety 
scores of 5.9 versus 5.7 for triglyceride chips and olestra chips, 
respectively, on a 9-point scale, with 9 being ``extremely full'' 
(p=0.07). Nor were any differences seen in beverage consumption, choice 
of beverage, or time since last meal prior to the movie between the two 
groups.
---------------------------------------------------------------------------
 
    \21\ In 1996, FDA estimated the probable life-time averaged 
intake of olestra at the 90th percentile to be 7.0 g/p/d. To 
evaluate subchronic conditions, FDA estimated that a ``high'' acute 
consumer of olestra (everyday for 12 weeks) would consume 20 g/p/d, 
equivalent to eating a 2 oz bag of potato chips every day, and the 
99th-percentile single-day intake of olestra for the group consuming 
the highest level of savory snacks to be 45 g/d (61 FR 3118 at 
3124).
---------------------------------------------------------------------------
 
    The petitioner attributed the lower chip consumption in the olestra 
group to the slightly lower preference for olestra chips reported by 
study participants. The petitioner stated, however, that the median 
consumption (2 oz) was more than a typical single-serving snack size 
bag of chips, and that approximately 100 participants ate more than 4 
oz of olestra chips (approximately 32 g of olestra).
    The petitioner reported that the proportion of subjects who 
reported GI symptoms after consuming olestra chips was not different 
from that after consuming triglyceride chips (15.8 percent and 17.6 
percent respectively). There were no differences between the olestra 
and triglyceride groups in the frequencies for 14 different self-
reported GI symptoms (gas, diarrhea, pain, cramping, upset stomach, 
loose stools, nausea, bloating, indigestion, aftertaste, eructation, 
constipation, vomiting, bloody stool), overall symptom severity for any 
GI event, nor time to onset or duration of symptoms. The petitioner 
also reported that consumption levels did not correlate with the rate 
of symptom reporting in either the olestra or triglyceride group.
    The petitioner planned to have 1,400 participants in the study and 
anticipated symptom reporting to be 10 percent for the triglyceride 
group and 15 percent for the olestra group. Using these assumptions, 
the study would provide 80 percent power for detecting
 
[[Page 46373]]
 
a 5 percent difference in the proportions of symptoms between the 
olestra and triglyceride groups. The final number of participants to 
complete the study was 1,092,\22\ which was fewer than planned. The 
rate of symptom reporting in the triglyceride group was 17.6 percent, 
which was higher than planned. Given the actual number of participants, 
and the actual rate of reports of symptoms in the triglyceride control 
group, FDA found that the study had an 80 percent chance of detecting a 
7 percent difference between the test groups (p=0.05) (Ref. 13).
---------------------------------------------------------------------------
 
    \22\ Of the 1,742 individuals originally enrolled for the study, 
1,123 kept their appointments. Thirty-one individuals could not be 
contacted for followup, leaving a total of 1,092 evaluable subjects.
---------------------------------------------------------------------------
 
    FDA observed that 962 participants completed a post-movie interview 
within the 2 to 4 days goal of the study. Of the remaining 130 
participants who were contacted, 124 participants were contacted in 5 
to 10 days, 3 on the day of the movie, 1 within a day, and 2 within 23 
days. FDA noted that P&G included data from these 130 participants in 
its analysis to enhance the sensitivity of its analysis.
    FDA noted that in both the olestra and triglyceride groups, the 
most frequently reported GI symptoms were abdominal pain, diarrhea, and 
flatulence. These symptoms are also the symptoms most commonly reported 
to P&G's passive surveillance program. FDA agrees with the petitioner 
that in this study, there was no difference in the rate or severity 
reported for loose stools or abdominal cramps between subjects who ate 
olestra-containing chips and subjects eating triglyceride chips. FDA 
examined the percent of subjects reporting at different levels of chip 
consumption and found that reports of diarrhea increased for both the 
olestra and triglyceride groups with increasing consumption of chips, 
but there was no difference in the rate of reporting between the groups 
(Refs. 10 and 13).
3. Home Consumption Study
    The Home Consumption Study \23\ was designed to measure, under 
market use conditions, the effect of eating chips made with olestra on 
GI symptoms in adults and children over an extended period of time 
(Ref. 14). This double-blind placebo-controlled trial represented 1,138 
households (3,181 individuals, ages 2 to 89) randomly assigned to 
either the olestra group or the control group. To be enrolled, at least 
half the members of the household had to have eaten corn or potato 
chips at least four times in the previous month and all members of the 
household had to be willing to participate in the 6-week long study. A 
contact for each household was identified and was required to return to 
the study site once a week for 6 consecutive weeks. During each visit, 
the contact could choose from a selection of potato chips and tortilla 
chip products labeled as containing either olestra or triglyceride. The 
selection of snacks used in the study were products available in the 
marketplace presented in typical packaging. To encourage snack 
consumption, up to eight bags of chips (varying in weight from 5.5 to 9 
oz) could be selected each week. For the households in the olestra 
group, the olestra-labeled packages contained olestra chips, but for 
the control group, the olestra-labeled packages contained triglyceride 
chips. For both groups, the triglyceride-labeled packages contained 
triglyceride chips. All olestra-labeled products displayed the olestra 
label statement.
---------------------------------------------------------------------------
 
    \23\ Dr. R. Sandler, Professor of Medicine, University of North 
Carolina, Chapel Hill, was the principal investigator for this 
study.
---------------------------------------------------------------------------
 
    At each weekly visit, the contact would also provide daily records 
kept by each member of the household regarding GI symptoms. The 
household contact assisted and/or completed the form for children. The 
record consisted of a check list of eight specific GI symptoms \24\ as 
well as a field to write in any other symptoms. On each day a GI 
symptom was recorded, the subject was to rate the effect of those 
symptoms on daily activity using a scale ranging from ``noticed but did 
not affect'' to ``missed all day at work/school.'' Medication use and 
physician visits were also to be recorded.
---------------------------------------------------------------------------
 
    \24\ The list of GI symptoms include the following descriptions: 
(1) Heartburn or indigestion, (2) nausea or queasiness, (3) 
vomiting, (4) gas, (5) bloating, (6) abdominal cramping or pains, 
(7) more frequent bowel movements, and (8) looser stool.
---------------------------------------------------------------------------
 
    There were 1,620 subjects from 568 households in the olestra group 
and 1,561 subjects from 570 households in the control group. The groups 
were similar with respect to age, sex, and race. Subjects ate chips 
frequently throughout the study. The median number of days on which a 
subject consumed an olestra-labeled chip was 20 days of a possible 42 
days for the olestra group and 21 of a possible 42 days for the control 
group. The length of the study and the large number of individuals per 
group resulted in a collective period of more than 30,000 ``eating'' 
days, making it possible to detect small differences in the reporting 
of GI symptoms. The median total amount of olestra-labeled chips eaten 
over the course of the study by the olestra group (25.2 oz) was 
slightly less than that eaten in the control group (27.6 oz). During 
the 42-day study, subjects whose consumption was in the top 10 percent 
of the olestra group ate more than 59 oz of chips, while in the control 
group, the top 10 percent of the group ate more than 70 oz of chips. 
The petitioner presented data to show that the rates of olestra 
consumption achieved were beyond customary snacking by comparing the 
intake of olestra at the 90th percentile of consumption in this study 
(13.3 g/d) to Market Research Corp. of America (MRCA) preapproval 
estimates (6.4 g/d), and to data collected regarding ``real-world'' 
olestra consumption in the Active Surveillance Study (2.1 g/d). The 
petitioner concluded that the rates of consumption achieved in this 
study for both the olestra and triglyceride groups were higher than 
usual snack consumption.
    The petitioner reported that for its original planned analysis for 
the study, which examined the percentage of eating days where GI 
symptoms were reported within 2 days, olestra-containing chips resulted 
in an increase (p<0.05) in the GI symptoms of more frequent bowel 
movements, loose stools, and gas. There was no increase in reports of 
abdominal cramping or any of the other individual or total GI symptoms. 
The petitioner decided that this analysis could not be clearly 
interpreted because olestra labeled chips were eaten on numerous days 
of the study and therefore a particular GI event would be associated 
with 2 or 3 eating days.
    The petitioner presented data from an analysis that compared the 
occurrence and frequency of GI symptoms between the olestra and control 
groups. The primary response variable was the percentage of individuals 
reporting a GI event. For all subjects who consumed olestra-labeled 
products, the petitioner found that there was no difference in the 
total percentage of subjects reporting a GI symptom between the olestra 
and control groups. Of the eight GI symptoms evaluated, the only 
difference was an increased number of reports of nausea for the control 
group. For those subjects who reported a GI event, the number of 
symptom days was also compared. When the petitioner examined the data 
by days on which subjects reported symptoms, there was a small increase 
in the olestra group in the number of days when more frequent bowel 
movements were reported (3.7 days for olestra compared to 2.8 days for 
controls; p=0.04). The petitioner calculated that this increase was 
about one symptom day out of the 42 days of the study. The petitioner 
reported that
 
[[Page 46374]]
 
subjects' self assessments showed little or no impact of GI symptoms on 
subjects' daily life, and there was no increase in the percentage of 
reported severe impacts in the olestra group compared to the control 
group.
    The petitioner also examined whether there were differences in the 
incidence of reported GI symptoms among the different age groups. The 
petitioner reported that there were no significant differences in total 
or specific GI symptoms between the olestra and triglyceride groups for 
children (2 to 12 years; n=885), teens (13 to 17 years; n=227), or the 
elderly (65 to 89 years; n=402), even among the highest consumers. This 
analysis showed that for adults (18 to 64 years; n=1667), there was an 
increased percentage in reporting the GI symptom gas in the olestra 
group compared to the control group. There was also an increase in the 
number of GI symptom days, and an increase in the number of more 
frequent bowel movement symptom days, among adult subjects eating 
olestra of approximately one symptom day out of the 42 days of the 
study.
    Among adult females in the olestra group, compared to adult females 
in the control group, there was an increase of approximately one 
symptom day out of 42 days of the study with regard to more frequent 
bowel movements, gas, and any GI symptom. The only difference regarding 
reports of abdominal cramping was an increase in the control compared 
to the olestra group for adult males.
    The petitioner concluded, based on the subjects' self assessments, 
that none of these reported increases in the number of symptom days 
were meaningful because there was no impact on subjects' daily 
activities. Based on its comparison of the percent of subjects who 
reported one or more GI events during the course of the study, P&G 
concluded that there were no meaningful or serious GI effects 
associated with eating olestra-containing chips.
    At the end of the 6-week study, P&G asked participants which kind 
of chips they thought they were eating from the olestra-labeled bags. 
P&G reported that the percentage of subjects reporting GI symptoms was 
greater (approximately 50 percent) in those who believed they were 
eating chips made with olestra compared to those who thought they were 
eating triglyceride chips. This was true regardless of whether the 
participant was actually eating olestra or triglyceride chips.
    FDA employed a number of statistical approaches to best address the 
different questions to be answered by the study, and while such 
differing approaches may yield different answers, this varied approach 
provides a more complete picture of the study results. FDA analyzed 
both the temporal relationship between consumption and symptoms, and 
summation data for the study (Refs. 15 and 16).
    Examination of temporal data is important for evaluating an 
association between olestra intake and GI symptoms. Such an analysis is 
also important because in a study of this length, subjects can modify 
their eating behavior based on their experience with a product. FDA 
found that subjects in both the olestra and triglyceride groups 
modified their intake of chips as a result of experiencing more 
frequent bowel movements. FDA was able to conclude that consumers 
modify their behavior based on their experience with olestra chips by 
examining the amount of chips consumed the day before, the day of, and 
the day after a report of more frequent bowel movements. Chip 
consumption decreased after experiencing more frequent bowel movements, 
although consumption of chips did not cease.
    In order to understand the temporal relationship between olestra 
consumption and GI symptoms, FDA examined the frequency of GI symptoms 
for numerous different patterns of olestra consumption over a period of 
several days.\25\ In all these analyses, FDA found that for men, 
olestra consumption resulted in an increase in any GI symptom, gas, and 
more frequent bowel movements, and a decrease in nausea. For women, 
olestra consumption resulted in an increase in any GI symptom, gas, 
looser stools, and more frequent bowel movements. On the day that chips 
were eaten, the difference in the percentage of occasions that more 
frequent bowel movements were reported for the olestra chips compared 
to the triglyceride chips was 1.6 percent for males and 1.2 percent for 
females. These effects were seen on days of consumption of olestra 
chips but not on subsequent days on which olestra-containing chips were 
not eaten. When olestra chips were consumed on consecutive days there 
was some cumulative effect for the reports of these GI symptoms. This 
was particularly true for males. For example, the difference in the 
percentage of occasions that a report was made in the category ``any GI 
symptom'' for the olestra chips compared to the triglyceride chips 
increased from 0.9 percent on the first day to 1.7 percent on the 
second day, to 2.6 percent on the third consecutive day that chips were 
eaten and a complaint was recorded. There was also a trend for more 
frequent and recent consumption of olestra to result in a GI symptom. 
While increasing consumption of olestra and triglyceride chips both 
resulted in more symptoms, the effect of olestra was greater compared 
to triglyceride chips at all doses.
---------------------------------------------------------------------------
 
    \25\ These included determining the percent of occasions for 
which GI symptoms occurred on the same day and the following 2 days 
of eating an olestra-labeled chip; comparing the frequency of 
occurrence of GI symptoms on days that olestra-labeled chips were 
eaten to days that chips were not eaten to determine a ``same day of 
eating effect''; determining the percent of days on which GI 
symptoms were reported for all non-eating days in order to evaluate 
possible delayed or continuing effects of olestra; comparing the 
percent of days on which GI symptoms were reported to the number of 
consecutive days eating olestra-labeled chips in order to examine 
possible cumulative effects; for various GI symptoms analyzing the 
pattern of consumption of olestra-labeled chips for the days prior 
to the GI symptom in order to examine how the most recent day of 
eating and the frequency of eating is related to the GI symptom; for 
various GI symptoms, determining the amounts of olestra-labeled 
chips consumed on the day the GI symptom occurred (Ref. 16).
---------------------------------------------------------------------------
 
    In examining the effect of olestra consumption on different age 
groups, FDA found that GI symptoms were primarily seen in the 18 to 64 
age group. There were no olestra-related effects in the groups over 65 
years or younger than 18 years.
    In a separate statistical analysis, FDA focused on the sum total of 
symptom days and consumption of olestra-labeled chips over the course 
of the 42-day study (summation data). FDA analyzed the data for each GI 
symptom for both the entire study population, and for a population 
divided based on age and gender.
    In the statistical analysis of the sum total of symptom days over 
the course of the 42-day study, FDA first examined the relationship 
between the reporting of particular GI symptoms and the consumption of 
olestra-containing foods by comparing the olestra group and the 
triglyceride group. FDA found that for all study subjects (males and 
females) over the course of the 42 day study, there was an increase of 
0.28 more frequent bowel movement symptom days in the olestra group 
compared to the triglyceride group. FDA then examined the relationship 
between the reporting of particular GI symptoms and the consumption of 
olestra-containing foods by analyzing the olestra group and the 
triglyceride group separately by gender. FDA found for females in the 
olestra group, there was an increase in ``any GI symptom'' of 0.5 mean 
symptom days compared to the females in the triglyceride control. It 
was also observed that for females in the olestra group, there was an 
increase of 0.3 symptom days in more frequent bowel
 
[[Page 46375]]
 
movements over the course of the 42 day study compared to females in 
the triglyceride group. For males in the olestra group, the analysis 
showed an increase of 0.24 more symptom days for more frequent bowel 
movements compared to males in the triglyceride group.
    FDA then examined the relationship between the amount of product 
consumed and symptoms reported for all study subjects (males and 
females), and found there were associations between olestra consumption 
and reports of ``any GI symptom'' (p=0.03), loose stools (p=0.006), and 
more frequent bowel movements (p=0.002). No such associations were 
observed between the consumption of the control chips (triglyceride 
chips labeled as olestra) and any measured symptom. When analyzed 
separately by gender, both sexes showed trends for an association 
between the consumption of olestra and loose stools (males p=0.001, 
females p=0.018), and more frequent bowel movements (males p=0.001, 
females p=0.042), but only males also showed a trend for an association 
between the consumption of olestra and ``any GI symptom'' (p=0.001).
    FDA examined the relationship between the consumption of olestra-
containing foods and reports of abdominal cramping. FDA found no 
difference in the frequency of reported abdominal cramping between the 
olestra group and the triglyceride group. FDA analyzed the olestra and 
triglyceride groups separately by gender for reports of abdominal 
cramping and found no difference between males or females in the 
olestra group as compared to the triglyceride group. FDA agrees with 
the petitioner that there was no observed difference in the incidence 
or association of reported abdominal cramps between the olestra group 
and the triglyceride group (Ref. 10).
4. Stool Composition Study
    The Stool Composition Study was sponsored \26\ by the petitioner as 
a followup to the preapproval Fecal Parameters Study (discussed 
previously in section II.A.2 of this document). The study was designed 
to establish whether consumption of olestra-containing foods is 
associated with changes in clinical measures of diarrhea (water and 
electrolyte loss), effects which may be harmful, or stool consistency 
alone, which may result from adding bulk to the stool and which is not 
harmful. In addition, the study was designed to determine the 
relationship between objective measures of clinical diarrhea (e.g., 
stool water output and bowel movement (BM) frequency) and subjective 
reports of ``diarrhea'' from study subjects. The effects of olestra 
were compared to a placebo, triglyceride chips, and to sorbitol, an 
osmotically active sugar alcohol that was chosen as a positive control 
to ensure that the study methodology was adequately sensitive to detect 
increases in stool water output.
---------------------------------------------------------------------------
 
    \26\ The GI consultant to the study was Dr. R. Gianella, 
University of Cincinnati.
---------------------------------------------------------------------------
 
    The study was a single-site, randomized, double-blind, placebo-
controlled parallel clinical trial. Sixty-six subjects, ages 18 to 74, 
were housed on a metabolic ward for 12 days and consumed meals ad 
libitum. The meals conformed to the American Heart Association Step I 
diet guidelines (no more than 30 percent of calories from fat). 
Beverages were available ad libitum. All study subjects had to consume 
5 oz of potato chips eaten as two afternoon snacks. A serving of potato 
chips was either olestra (test) or triglyceride (placebo). All subjects 
were also required to consume 1.5 oz of candy made either with sorbitol 
(test) or sucrose (placebo) as a morning snack. The first two days 
(study days 1 and 2) were a lead-in period during which subjects were 
acclimated to the living conditions and the diet, and consumed placebo 
snacks (triglyceride potato chips and sucrose candies). Stool samples 
were not collected during the lead-in period. The next 4 days (study 
days 3 to 6) comprised the baseline period, in which subjects continued 
to consume placebo snacks, and all stool samples, BM ratings, and GI 
symptoms were collected. For the final 6 days (study days 7 to 12), 
subjects consumed snacks according to their randomly assigned treatment 
group, and all stool samples, bowel movement ratings, and GI symptom 
reports were collected. There were two olestra test groups (20 g and 40 
g olestra) and two control groups (positive control of 40 g sorbitol 
and placebo). The placebo group consumed two servings of placebo 
(triglyceride) potato chips and placebo (sucrose) candy. The positive 
control group consumed two servings of placebo potato chips and test 
candy (40 g sorbitol). The 20 g olestra test group consumed one serving 
of test potato chips (olestra), one serving of placebo potato chips, 
and placebo candy. The 40 g olestra group consumed two servings of test 
chips and placebo candy.
    The petitioner noted that in the study the doses of olestra were 
threefold to sixfold more than the estimated daily intake, and 10 to 20 
times more than the observed intake at the 90th percentile level in the 
Active Surveillance Study (see section III.D.1 of this document). The 
high dose, 40 g/d, was higher than the highest dose used in the 
preapproval nutrition studies (32 g/d) described previously in section 
II.A.3 of this document, in which the high dose group experienced an 
increase in GI symptoms, specifically in reported diarrhea/loose 
stools. In that preapproval study, FDA concluded that the reported 
diarrhea was not diarrhea in the medical sense because there was no 
evidence of subjects experiencing significant fluid or electrolyte loss 
(hemoconcentration, electrolyte imbalance; 61 FR 3118 at 3152-3154).
    The petitioner concluded that with regard to the critical 
parameters that are medically relevant in defining diarrhea, the 
objective measures showed that olestra did not meaningfully change 
either the total stool output or stool water output, while sorbitol 
produced large effects on both parameters. Compared to baseline, mean 
stool water output increased 9 g/d and 37 g/d for the 20 and the 40 g/d 
olestra groups respectively, and 325 g/d for the 40 g/d sorbitol group. 
Stool water output decreased 28 g/d for placebo. The measured mean 
stool water content for the sorbitol group was nearly 10 times greater 
than the group consuming the highest level of olestra and the number of 
watery BMs was 140 in the sorbitol group, one in the 40 g/d olestra 
group, none in the 20 g/d, and one in placebo. While sorbitol 
significantly increased the severity of abdominal cramping compared to 
placebo, olestra did not. The petitioner found that olestra consumption 
did not result in any clinically meaningful increases in objective 
measures of diarrhea, namely, total stool output, bowel movement 
frequency, and stool water and electrolyte output. The mean number of 
BMs for the olestra 40 g/d group was increased compared to placebo but 
was not increased compared to the olestra 20 g/d group. Subject reports 
of ``watery, difficult to control diarrhea'' did not necessarily 
correlate with measured viscosity of the stool. Olestra did increase 
stool weight in proportion to the amount eaten, and daily consumption 
of olestra gradually softened stool in a dose-responsive manner. The 
sponsor found that there was increased reporting of ``diarrhea'' in the 
olestra treatment groups during the treatment phase without an increase 
in total water output outside the normal range, i.e., the range 
observed during the baseline period and in the placebo group.
    P&G concluded, based upon the study results, that the consumption 
of olestra
 
[[Page 46376]]
 
does not cause diarrhea, but simply adds bulk and softening to the 
stool.
    FDA reviewed the data from this study and agrees with the 
petitioner's analysis, although some of the agency's analytical 
strategies differed from those of the sponsor (Ref. 17). FDA concludes 
that both comparisons of the mean after treatment and of changes from 
baseline showed dose responsive increases in stool characteristics 
(total output, water output, consistency, frequency and increases in 
water content) that were not clinically significant (Ref. 18).
    Using a 7-point scale to rate consistency of bowel movements (1 = 
watery, diarrhea; 4 = normal; 7 = hard, constipation), subjective 
ratings of stool consistency showed that subjects who ate 40 g/d 
olestra perceived their stools to be looser (mean rating 2.4) compared 
to those who ate 20 g/d olestra (mean rating 3.1). By comparison, 
placebo subjects had a mean score of 3.9 whereas those subjects in the 
40 g/d sorbitol group had a mean score of 1.5 (mean scores determined 
for days subjects consumed snacks according to their randomly assigned 
treatment group). When stool consistency was measured by peak force 
value for extrusion, both olestra groups had a lower mean stool 
consistency than placebo and the 40 g/d olestra group was lower than 
the 20 g/d group. These dose responsive findings seen among subjects 
eating olestra resulted from gradual stool softening effects observed 
after several consecutive days of olestra consumption. Although 
subjects characterized these viscosity changes as ``diarrhea,'' the 
changes were not associated with an increase in stool water.
    FDA examined the percentage of symptom days for cramping and found 
that although the 40 g/d olestra group reported an increased incidence 
of abdominal cramping compared to those in the 20 g/d olestra group 
(35.8 percent compared to 9.8 percent), this difference did not rise to 
statistical significance. The percentage of subjects reporting 
abdominal cramping in the 20 g/d olestra group appeared to decrease 
when compared to baseline or placebo (9.8 percent compared to 20.5 
percent or 18.3 percent). The 40 g/d sorbitol group had the highest 
percentage (69.8 percent) of reports of cramping. Subjects rated 
symptom severity on a scale of 0 to 5, with 0 representing none and 5 
extreme. The severity of cramps reported by subjects in the olestra 40 
g/d group was less severe than that reported by subjects in the 40 g/d 
sorbitol group (0.72 compared to 2.3). No significant olestra effects 
were found for GI symptom severity, although one individual in the 20 
g/d olestra group reported severe urgency at a rating higher than any 
other report in any of the other groups (Refs. 10 and 18).
5. Comments Regarding the GI Studies
    FDA received comments about the new GI studies. FDA considered 
these comments and responds in the following paragraphs. Comments 
regarding the label statement for GI effects will be discussed in 
section V of this document.
    (Comment 5) A comment from CSPI to the current petition criticized 
the Rechallenge Study. The comment stated that the study subjects were 
not screened for sensitivity to olestra, as was done in the preapproval 
Fecal Parameters Study. The comment also asserted that the Rechallenge 
Study contained a strong likelihood of bias because only 10 percent of 
those contacted agreed to participate in the rechallenge and those that 
did participate consumed olestra on only 2 days, at least 1 week apart, 
which reduced the sensitivity of the study. CSPI asserted that the 
Rechallenge Study also assumed that those sensitive to olestra would 
respond to it 100 percent of the time. The comment contended that those 
experiencing adverse reactions may only do so under certain 
circumstances, not 100 percent of the time.
    FDA does not agree that the selection of study subjects biased the 
Rechallenge Study nor does CSPI provide such evidence. FDA has 
determined that the subjects who participated in the Rechallenge Study 
were adequately representative of those persons who contacted the 
postmarketing surveillance system in terms of severity of initial 
symptoms and amount of olestra reportedly consumed prior to the initial 
symptom episode (Ref. 11). Further, CSPI provided no basis for its 
assertion that additional subject screening is necessary to accomplish 
the objectives of the Rechallenge Study.
    CSPI states that the sensitivity of the Rechallenge Study was 
reduced because participants consumed olestra on only 2 days, at least 
1 week apart. The conditions of the study were designed to be similar 
to the conditions under which the subjects originally reported effects 
that they attributed to consuming an olestra-containing snack. FDA 
found that for nearly three-quarters of the subjects, the amount of 
olestra consumed in the study was comparable to, or greater than, the 
amount associated with their initial symptom episode (Ref. 11). In 
addition, more than three-quarters of the subjects reported that their 
initial symptom episode occurred after a single eating occasion. 
Therefore, subjects were challenged with 2 oz of olestra chips on two 
occasions separated by a week, providing a dose and number of exposures 
comparable to, or greater than, those associated with many of the 
subjects' initial symptom episodes.
    CSPI's comment did not reference where FDA or the petitioner 
assumed that those sensitive to olestra would respond to it 100 percent 
of the time, nor is FDA aware of anyone who has put forth such a 
position. Indeed, FDA agrees that even if an individual experiences a 
reaction to olestra, that individual may not experience such reaction 
after every exposure. The Rechallenge Study shows that subjects exposed 
to olestra containing-chips were no more likely to report GI symptoms 
than when exposed to an equal amount of triglyceride chips. Thus, the 
study subjects' reactions to olestra containing-chips are not so 
frequent that they can be distinguished from their reactions to regular 
chips under the conditions of the test.
    (Comment 6) A comment from CSPI to the current petition criticized 
the Acute Consumption Study. CSPI's comment relies on its published 
letter \27\ commenting on a published study (Ref 12.) that reports data 
from the Acute Consumption Study. CSPI stated that the study may have 
failed to detect the true incidence of GI effects due to a lack of 
statistical power or inadequate controls. For example, with the 
incidence of ``any GI event'' of about 15 percent, 550 subjects in each 
group would have provided only about a 50 percent probability of 
detecting a 5 percent actual increase in the treatment group. Along the 
same lines, diarrhea and loose stools were increased less than 1 
percent in the olestra group compared to baseline levels of 2.6 percent 
and 1.1 percent, respectively. The comment asserted that maintaining 80 
percent power to detect a 1 percent increase over a 2 percent baseline 
requires about 4,000 subjects per group. The comment also contends that 
the darkened movie theater may potentially cause exposure 
misclassification (some ``olestra eaters'' may have eaten few or none 
of their chips; some ``non-olestra eaters'' may have eaten friends' 
olestra chips). The comment also stated that it took up to 10 days 
after consumption to assess symptoms. CSPI also pointed out that non-
olestra eaters consumed one-third more chips than the olestra eaters.
---------------------------------------------------------------------------
 
    \27\ CSPI's published letter was included in the comment as an 
attachment (Ref. 19).
---------------------------------------------------------------------------
 
    The criticism by CSPI of the Acute Consumption Study does not 
negate the
 
[[Page 46377]]
 
conclusion that FDA reached in its analysis of the study. The Acute 
Consumption Study was conducted to provide information relevant to 
whether olestra-containing foods should bear a label statement that 
informs consumers about the potential GI effects associated with 
olestra. FDA points out that the Acute Consumption Study was only one 
of several studies under consideration in this petition, and that the 
agency's decision on the petition is based on the totality of evidence 
in the record.
    While the petitioner's Acute Consumption Study did not achieve the 
statistical power that P&G originally desired (80 percent power to 
detect a 5 percent difference between treatment groups), the study 
still provides meaningful information concerning the effect of olestra-
containing foods on the GI system. FDA's scientific review determined 
that the study does have 80 percent power to detect a 7 percent 
difference between treatment groups (Ref. 13). The study showed that 
there was no difference in the rate or severity of loose stools or 
abdominal cramps between subjects who ate olestra-containing chips 
compared to those who ate triglyceride-containing chips.
    The comment provides no evidence that the darkened theater or the 
method used to collect symptom data affected the outcome of the study. 
As discussed previously, the study protocol was designed to minimize 
the possibility of inaccurate measurements or subjects' sharing of 
chips. For example, study participants were instructed to be seated in 
the theater at least one seat away from other participants and not to 
share their chips or beverage with anyone else. The theaters were also 
monitored by several staff during the movie.
    Similarly, the comment did not explain the effect on the study 
results, if any, from the 10-day period used to assess symptoms. After 
the movie, trained telephone interviewers contacted study participants 
and administered a recall questionnaire to collect information on any 
effects experienced since the movie. The study protocol specified that 
participants be contacted within 2 to 4 days of viewing the movie. The 
petitioner reported that 85 percent of study subjects (962 of the 
1,092) were contacted within 2 to 4 days of viewing the movie, an 
additional 124 subjects were contacted in 5 to 10 days.\28\
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    \28\ Of the remaining subjects, three were contacted on the day 
of the movie, one within a day, and two within 23 days (Ref. 13).
---------------------------------------------------------------------------
 
    FDA agrees that the median chip consumption for the control group 
was greater than that for the olestra group. As discussed previously, 
the Acute Consumption Study was designed to be an ad libitum study, 
allowing the investigators to examine the effects of customary or usual 
consumption. As an ad libitum study, it is possible that one group of 
subjects may consume more chips than the other. For example, the median 
consumption of chips made with olestra was 2.1 oz compared to 2.7 oz 
for chips made with conventional triglycerides. CSPI did not explain 
how the fact that one group of subjects ate more chips than the other 
affects the conclusions drawn from this study regarding the need for 
special labeling.
    (Comment 7) A comment from CSPI to the current petition criticized 
the Home Consumption Study. CSPI's comment relies on its published 
letter \29\ commenting on a published study that reports data from the 
Home Consumption Study (Ref. 14). The comment raises five issues: (1) 
The comment stated that some of the data relating to the highest decile 
of olestra consumers were overlooked; (2) the comment argued that it is 
important to focus on the small number of heavier consumers because 
most subjects ate relatively few olestra-containing chips; (3) the 
comment stated that in the highest decile of olestra consumers the 
incidence of more frequent bowel movements and loose stools was twice 
that of controls; (4) the comment stated that olestra consumers in the 
highest decile had symptoms on 18 percent of person-days, compared to 
12 percent of person-days in the control group (table 4 in Ref. 14); 
and (5) the comment pointed out that olestra consumers missed some or 
all of their activities on 0.4 percent of days, compared to 0.2 percent 
in the control group.
---------------------------------------------------------------------------
 
    \29\ CSPI's published letter was included in its comment as an 
attachment (Ref. 20).
---------------------------------------------------------------------------
 
    Prior to publication of the article concerning the Home Consumption 
Study (Ref. 14), FDA conducted its own indepth analysis of the raw data 
from the Home Consumption Study (Refs. 15 and 16) and described this 
analysis at the 1998 FAC meeting in which CSPI participated. FDA's 
analysis included an estimate of the extra symptom-days experienced by 
subjects in both the 90th and 95th percentile of olestra-containing 
chip consumption (Ref. 15). Subjects at the 90th percentile ate 64 oz 
of olestra-containing chips over the course of the study while those at 
the 95th percentile ate 83 oz of olestra-containing chips over the 
course of the study. Although CSPI alleges that the subjects in the 
study ate relatively few olestra-containing foods, the petitioner 
presented data to show that, in fact, the rates of olestra consumption 
achieved in the study were beyond usual snack consumption.
    As part of the Home Consumption Study, the investigators considered 
the effect of GI symptoms on subjects' daily activities. In its 
comment, CSPI points out that olestra consumers missed some or all of 
their activities on 0.4 percent of days, compared to 0.2 percent in the 
control group, implying that this is significant. FDA disagrees.
    CSPI does not explain how it calculated the percentage of days on 
which subjects missed some or all of their activities, nor does CSPI 
provide statistical analyses to assess whether these differences 
occurred by random chance (e.g., illness unrelated to olestra). FDA was 
able to replicate the numbers that CSPI presented and performed tests 
of statistical significance on the data. The actual number of days on 
which subjects in the highest decile missed some or all of their 
activities is very small (9 of 2,226 days in the olestra group versus 5 
of 2,646 days in the control group). Five subjects in the olestra group 
and four subjects in the control group missed some or all activities at 
least 1 day. The number of subjects missing activities and the number 
of days missed by these subjects are comparable for the olestra and 
control groups, except for one subject in the olestra group who missed 
some or all activities on 4 days (Ref. 21).\30\ From these data, it 
cannot be concluded that for the highest decile of consumers olestra 
consumption resulted in an increase in days in which consumers missed 
some or all activities. FDA believes that the Home Consumption Study, 
designed to examine the effects of ``real life'' olestra consumption, 
provides useful information relevant to the labeling of olestra-
containing foods. CSPI does not show how their analysis would change 
FDA's conclusions.
---------------------------------------------------------------------------
 
    \30\ Sophisticated statistical models are impractical for such a 
small number of cases. However, a Fisher's Exact test showed that 
the proportion of subjects in the olestra group who missed some or 
all activity at least 1 day was not significantly different (p-value 
of 0.73) from the proportion of subjects in the control group who 
missed some or all activity at least 1 day.
---------------------------------------------------------------------------
 
    (Comment 8) A comment from CSPI to the current petition criticized 
the petitioner's Stool Composition Study. The comment stated that this 
study does not negate and should not supersede the two preapproval 8-
week studies or the preapproval Fecal Parameters Study. In its comment, 
CSPI cites a 1995 FDA memorandum discussing the Fecal Parameters Study 
(Ref. 22) and asserts that the memorandum says that several
 
[[Page 46378]]
 
subjects in the study experienced high rates of water loss through 
their stool. The comment also stated that the definition of diarrhea 
used in the Stool Composition Study was too narrow and is not 
consistent with the definition used by the Centers for Disease Control 
and Prevention (CDC; three or more loose stools in a 24 hour period). 
The comment asserted that self-reporting is usually considered 
sufficient to conclude that people experience diarrhea regardless of 
demonstrated loss of electrolytes.
    In contrast to the Acute Consumption Study, the Home Consumption 
Study, and the Rechallenge Study, the Stool Composition Study was 
designed to extend the understanding of olestra's effect on stool 
characteristics that would potentially represent a safety concern. For 
this reason, the Stool Composition Study was conducted under conditions 
most likely to elicit GI effects. The highest dose of olestra provided 
in the Stool Composition Study (40 g/d) was greater than the 32 g/d 
used in the preapproval 8-week studies which was shown to cause an 
increase in GI symptoms (specifically in reported diarrhea/loose 
stools) and was twice as high as the highest dose given in the 
preapproval Fecal Parameters Study (20 g/d). Additionally, subjects' 
stool samples were collected for all 6 days of the treatment period in 
the Stool Composition Study, compared to only three days of the 7-day 
treatment periods in the Fecal Parameters Study. The Stool Composition 
Study does not negate the preapproval studies, but the results of the 
preapproval studies must be considered in light of those from the Stool 
Composition Study.
    The results of the Stool Composition Study show that olestra 
consumption does not result in any clinically meaningful increases in 
the objective measures of diarrhea. Importantly, the Stool Composition 
Study assessed the effects of olestra consumption using objective 
parameters such as total stool output, bowel movement frequency,\31\ 
and stool water and electrolyte output rather than a subject's 
subjective assessment of whether he or she experienced diarrhea. The 
use of objective measures of diarrhea is necessary to assess whether 
the ``diarrhea'' experienced by study subjects represents a safety 
concern.
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    \31\ FDA notes that the mean bowel movement frequencies in the 
olestra-consuming groups were less than three bowel movements per 
day. The mean bowel movement frequencies were 1.6 +/- 0.2 BM/d (mean 
+/- standard error) in the 20 g/d olestra group and 2.0 +/- 0.2 BM/d 
(mean +/- standard error) in the 40 g/d olestra group (Ref. 18).
---------------------------------------------------------------------------
 
    FDA was concerned with the potential for olestra to cause diarrhea 
because diarrhea of medical significance is associated with excessive 
water loss and electrolyte loss, which may raise safety concerns. The 
Fecal Parameters Study memorandum cited by the comment states that the 
stool water concentration of subjects who reported having diarrhea 
during the olestra 20 g/d period did not differ from that of their 
nondiarrheal stools during the placebo period. The memorandum also 
states that although the percent of water in the stools may not have 
differed, it is possible that absolute water loss was greater in 
subjects reporting olestra-associated diarrhea because of the greater 
mass (weight) of stool passed. FDA concluded in the 1996 final rule 
that the loose stools experienced in the preapproval clinical studies 
were not diarrhea in the medical sense because they were not associated 
with loss of water or electrolytes (61 FR 3118 at 3159). The agency 
also stated that even those subjects in the 8-week studies who 
experienced loose stools or diarrhea continuously for several weeks 
during olestra consumption did not show any evidence of fluid loss such 
as hemoconcentration or electrolyte imbalance. Thus, the agency 
determined that olestra-related GI effects were not adverse health 
effects (61 FR 3159). The results of the Stool Composition Study 
confirm the agency's 1996 decision that the GI effects resulting from 
olestra consumption do not represent adverse health effects, regardless 
of the terminology (diarrhea or otherwise) used to describe these 
effects.
 
D. A Study Regarding Nutritional Effects--Active Surveillance
 
    As discussed previously in section II of this document, olestra is 
neither digested nor absorbed, and as such, passes intact through the 
digestive tract where it can interact with fat-soluble dietary 
components present in the gut at the same time. Fat-soluble nutrients 
and components tend to partition or dissolve into the olestra, thereby 
reducing the absorption efficiency of these substances (61 FR 3118 at 
3144-3149). Olestra does not interfere with the absorption of macro-
nutrients (protein, carbohydrates, and fats) or water-soluble nutrients 
(61 FR 3118 at 3149-3152). The clinical studies conducted in support of 
the 1996 final rule examining the effect of olestra on fat-soluble 
components of the diet were performed under conditions that maximized 
the interaction of olestra with these dietary components, i.e., olestra 
was incorporated into foods eaten at every meal. These studies were not 
designed to examine effects from the usual or customary consumption of 
savory snacks made with olestra (see section II.A.3 of this document).
    To compensate for the effect of olestra on the absorption of the 
fat-soluble vitamins A, D, E, and K, FDA required that these vitamins 
be added to olestra-containing foods. The level of addition was chosen 
to ensure that there would be neither a reduction in the absorption of 
fat-soluble vitamins from the diet, nor an increase in vitamin levels 
due to the presence of the added vitamins in the olestra-containing 
foods (see section II.A.3 of this document). Although FDA noted that 
olestra interferes with the absorption of carotenoids, FDA found no 
scientific basis for requiring the addition of any carotenoid to 
olestra-containing foods (61 FR 3118 at 3147-3149).
    As outlined by the petitioner in its January 24, 1996, letter to 
the agency, P&G established a program of active surveillance. A report 
of this surveillance with results and analysis from the first year at 
the sentinel site was submitted to the agency on April 15, 1998. 
Additionally, the agency has continued to review and evaluate new data 
and information that bear on the safe use of olestra, such as new data 
and information on the health significance of carotenoids.
1. Active Surveillance Study by P&G
 
    The petitioner provided funding to investigators at the Fred 
Hutchinson Cancer Research Center in Seattle, WA, to design and 
implement a multi-year, Active Surveillance Study to monitor patterns 
of use of olestra-containing savory snack products and to collect blood 
samples to measure nutrient status (Ref. 23). The study had three 
specific goals: (1) To monitor adoption and patterns of use of olestra-
containing savory snack products in representative samples of the U.S. 
population; (2) to assess the association between the introduction of 
olestra-containing savory snacks and serum concentrations of 
carotenoids and fat-soluble vitamins in representative cross-sectional 
samples of the U.S. population; and (3) to assess the long-term 
association between consumption of olestra-containing savory snacks and 
serum concentrations of carotenoids and fat-soluble vitamins among a 
cohort of olestra consumers.
    The study has three components corresponding to the three specific 
aims. The first component, called the population cross-section, was a 
telephone survey used to monitor the prevalence and patterns of 
olestra-containing savory snack consumption,
 
[[Page 46379]]
 
fruit and vegetable consumption, and triglyceride savory snack food 
consumption by consumers. Demographic information was collected as 
well. A telephone survey was conducted in each of the study sites 
before olestra-containing snacks were marketed. Subsequent yearly 
surveys were completed after olestra-containing snacks were introduced 
to the market.
    A random sample of participants in each telephone cross-section 
sample was recruited into the second component, a clinical cross-
section. The clinical cross-section was an investigation of the 
relationships among nutrient intake, olestra consumption, and serum 
nutrients. Study participants visited a clinic to provide further 
information, including dietary information, medical histories, and 
blood samples. Followup telephone interviews included questions about 
usual fruit, vegetable, and snack food use during the previous month, a 
24-hour dietary recall to measure co-consumption of fruits and 
vegetables with savory snacks, health symptoms and status, and a short 
household food inventory.
    Within the clinical cross-section, information on olestra intake 
was used to select olestra users from non-users to be recruited into 
the third component of the Active Surveillance Study, i.e., the 
clinical cohort study. The clinical cohort study was an investigation 
of the relationships among nutrient intake, olestra consumption, and 
changes in serum nutrients over time. Participants in the clinical 
cohort are a subset of those people who participated in the Year 0 
clinical cross-section and were monitored annually over the course of 
the Active Surveillance Study. The clinical cohort was designed to have 
an over-representation of consumers of olestra-containing snack food. 
The design for the clinic visit and the information gathered is the 
same as for the clinical cross-section.
    The study was conducted in four U.S. cities. As of the publication 
of this document, data are available only from the sentinel site, 
Marion County, IN, where test marketing began in 1997.\32\ The study 
began one year later in the other cities, because national marketing of 
olestra-containing foods in those areas began later.
---------------------------------------------------------------------------
 
    \32\ The other three cities in the Active Surveillance Study 
were Baltimore, MD, San Diego, CA, and Minneapolis, MN.
---------------------------------------------------------------------------
 
    The first component of the active surveillance is the population 
cross-section. A random-digit-dial telephone survey of Marion County, 
IN, residents was completed before olestra-containing foods were 
marketed in that area (February 1997). This survey (Year 0) included 
1,962 adults, aged 18 years and over. The second telephone survey was 
completed after olestra-containing foods were introduced to the local 
market (between August 1997 and January 1998). This survey (Year 1) 
included 1,525 adults, aged 18 years and over. Based on the Year 1 
data, which are weighted to be representative of the Marion County 
population, 15.5 percent of adults reported eating olestra-containing 
snacks one or more times per month with the median frequency being 
three times per month. Ninety percent of adults reported eating one or 
more servings of fruits and vegetables per day, thus providing a basis 
for assessment of any effects on dietary carotenoid absorption. Intake 
of fruits and vegetables and intake of total snacks did not change in 
the population cross-section between Year 0 and Year 1. Olestra-
containing snack food introduction was not associated with an overall 
increase in savory snack consumption or with a decrease in fruit and 
vegetable intakes. There was a modest decrease in consumption of 
reduced- and non-fat savory snacks at Year 1 compared to Year 0.
    Blood sera from study subjects, in both the cross-sectional and 
clinical cohorts, were analyzed for vitamins A, D, E, and K, total 
cholesterol, high density lipoprotein (HDL) and triglycerides, and the 
six major carotenoids that represent more than 90 percent of the 
circulating carotenoids (alpha and beta carotene, lycopene, lutein, 
zeaxanthin, and beta-cryptoxanthin). The study investigators then 
compared these serum measures based on olestra intake. Four olestra 
consumption groups were defined: (1) None; (2) low (less than 0.4 g/d 
of olestra, which is less than the 60th percentile of consumption); (3) 
medium (between 0.4 and 2.0 g/d of olestra, which is between the 60th 
and 90th percentiles of consumption); and (4) high (greater than 2 g/d, 
which is greater than the 90th percentile of consumption).
    Results from the cross-sectional study comparing 1,252 subjects in 
year 0, and 1,164 subjects in year 1, show that with increasing olestra 
intake, there were significant trends for an increase in vitamin K 
levels (p = 0.013) and a decrease in serum cholesterol (p = <0.05). 
There were no significant differences or trends found for other 
vitamins or for total carotenoid or individual carotenoids that could 
be associated with olestra consumption.
    For the clinical cohort (477 study participants), the sponsor 
reported that for the entire cohort from year 0 to year 1, there was a 
decrease in mean serum concentrations of total carotenoids, as well as 
in concentrations of retinol, 25-OH vitamin D, lycopene, lutein, and 
zeaxanthin, and an increase in beta-cryptoxanthin. Tests of association 
between olestra consumption and changes in serum concentrations of fat-
soluble vitamins and carotenoids were based on regression models that 
included variables to characterize the four levels of olestra 
consumption. However, these changes were not related to the amount of 
olestra consumed. A trend was observed for increased vitamin K, but the 
change did not reach statistical significance (p = 0.087). There were 
no changes observed for the other vitamins.
    The petitioner cautioned that the results discussed previously 
reflect data from only the first year that olestra products were 
marketed, and that data were available from only a single site. With 
these caveats, the petitioner reached the tentative conclusion that it 
appeared that the consumption of olestra-containing foods in the 
marketplace had little, if any, effect on the status of fat-soluble 
vitamins and nutrients as measured by serum concentration.
    FDA notes that survey results show that the co-consumption of 
savory snacks (made with or without olestra) with a fruit or vegetable 
was relatively rare. Overall, less than 15 percent of total carotenoids 
were consumed with any savory snack. Olestra's effect on the absorption 
of fat-soluble carotenoids is greatest when co-consumed with the source 
of the carotenoid. Interference with absorption of carotenoids 
diminishes and then disappears as the time between eating an olestra-
containing food and a carotenoid-containing product increases.\33\
---------------------------------------------------------------------------
 
    \33\ The precise length of time olestra interferes with 
absorption varies with the dose of olestra, and also varies somewhat 
from individual to individual, as GI transit time is variable among 
individuals (61 FR 3118 at 3144).
---------------------------------------------------------------------------
 
    In the clinical cross-sectional sample, 217 of 947 individuals 
reported eating at least one olestra-containing food in the previous 
month with a median intake of 8.1 g of olestra per month. The 90th 
percentile consumption level was 64 g of olestra per month. Of the 402 
clinical cohort participants who were considered consumers of olestra, 
only 139 reported eating any olestra-containing foods in the previous 
month. The median frequency of eating olestra-containing foods for this 
group of consumers was 1.01 times per month with a median intake of 
11.9 g of olestra per month. The 90th percentile
 
[[Page 46380]]
 
frequency of eating olestra-containing foods was six times per month 
with a 90th percentile intake total of 70.6 g of olestra per month.
    FDA notes the infrequent and small olestra ingestion reported in 
the study. These